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Page 1

as) United States
cz) Patent Application Publication 0) Pub. No.: US 2024/0301032 Al

Hasan et al.

US 20240301032A1

(43) Pub. Date: Sep. 12, 2024

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SUBSTRATES COMPRISING ELASTIN-LIKE
POLYPEPTIDES AND CALCIUM IONS

Applicant: MINTECH-Y, LLC, WILMINGTON,
DE (US)

Inventors: Abshar Hasan, Nottingham (GB);
Sherif Ahmed Abdelsalam
Elsharkawy, London (GB); Alvaro
Mata Chavarria, Nottingham (GB)

Assignee: MINTECH-V, LLC, WILMINGTON,

DE (US)
Appl. No.: 18/434,379
Filed: Feb. 6, 2024

Related U.S. Application Data

Provisional application No. 63/483,475, filed on Feb.

6, 2023.

Publication Classification

(51) Int. Cl.
CO7K 14/78 (2006.01)
C30B 7/04 (2006.01)
(52) US. CL
CPC... . CO7K 14/78 (2013.01); C30B 7/04

(2013.01)

(57) ABSTRACT

The disclosure is directed towards polypeptide substrates
and methods of synthesis thereof. Such substrates can be
embedded with calcium ions from a number of ionic
sources. These calcium-embedded, polypeptide substrates
can be used to grow a variety of crystal structures including,
flower-shaped, onion-shaped, and needle-like crystal struc-
tures. As such, the disclosure is additionally directed
towards methods of crystal growth from polypeptide sub-
strates. Compositions of the disclosure can be used in a wide
variety of medical and other applications.

Specification includes a Sequence Listing.

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US 2024/0301032 Al

SUBSTRATES COMPRISING ELASTIN-LIKE
POLYPEPTIDES AND CALCIUM IONS

PRIORITY AND INCORPORATION BY
REFERENCE

[0001] This application claims priority to U.S. Provisional
Application Ser. No. 63/483,475, filed on Feb. 6, 2023, the
entire disclosure of which is hereby incorporated by refer-
ence herein for any and all purposes. This application hereby
incorporates by reference the entire disclosure of U.S. patent
application Ser. No. 17/588,579, filed on Jan. 31, 2022,
including the sequence listings by reference herein for any
and all purposes.

SEQUENCE LISTING

[0002] The application contains a Sequence Listing which
has been submitted electronically in XML format and is
hereby incorporated by reference in its entirety. Said .XML_
copy, created on May 16, 2024, is named “067608-
0002US1” and is 51 kilobytes in size. The sequence listing
contained in this .XML file is part of the specification and is
hereby incorporated by reference herein in its entirety.

TECHNICAL FIELD OF INVENTION

[0003] The present invention relates to polypeptide sub-
strates incorporating calcium ions and processes for their
formation. The present invention also relates to crystals
produced from these substrates and processes for their
production.

BACKGROUND

[0004] Elastin-like polypeptides (ELPs) are a type of
protein-like molecule that consist of repeating pentapeptide
sequences of Val-Pro-Gly-Xaa-Gly (VPGXG), where X is
any amino acid apart from proline. These molecules undergo
a phase transition at a certain transition temperature (T,),
which results in the transition from a soluble to an insoluble
form. In solutions with a temperature lower than T,, free
polymer chains remain in an unordered state showing full
hydration (the soluble form). In solutions with temperatures
exceeding Tt, polymer chains show a more ordered structure
(known as the B-spiral), stabilized by hydrophobic interac-
tions and intramolecular type B structures increasing the
association of polymer chains.

[0005] However, ELP membranes are limited in their
ability to access more varied crystal morphologies and form
crystal structures inside the membrane.

[0006] Therefore, there exists a need to address limitations
of membranes existing in the art.

SUMMARY

[0007] It is to be understood that this summary is not an
extensive overview of the disclosure. This summary is
exemplary and not restrictive, and it is intended to neither
identify key or critical elements of the disclosure nor delin-
eate the scope thereof. The sole purpose of this summary is
to explain and exemplify certain concepts of the disclosure
as an introduction to the following complete and extensive
detailed description.

[0008] The present disclosure relates to a polypeptide
substrate which can form crystal structures on both the

Sep. 12, 2024

interior and exterior of the membrane. Such substrates can
be embedded with calcium ions.

[0009] The present disclosure relates to a polypeptide
substrate which can form more varied crystal structures
including flower-shaped, onion-shaped, and needle-like
crystals.

[0010] The present disclosure relates to providing crystals
having improved stiffness, toughness, hardness, wear resis-
tance, compressive strength, and acid resistance.

[0011] The present disclosure relates to a process of grow-
ing the mineralized structures epitaxially from underlying
crystal structures. Underlying crystal structures include bone
tissue and surrounding dental enamel. This is facilitated by
the incorporation of calcium ions into polypeptide sub-
strates.

[0012] The present disclosure relates to a process for
forming a crystal structure from a polypeptide substrate
incorporating calcium ions.

[0013] The present disclosure relates to increased forma-
tion of amyloid-like ensembles from polypeptide molecules
using Ca ions.

[0014] The present disclosure relates to incorporating
polypeptide substrates with or without crystal structures into
a variety of devices and applications.

[0015] The present disclosure relates to methods and com-
positions for overcoming or mitigating at least one problem
of the prior art, whether expressly disclosed herein or not.

BRIEF DESCRIPTION OF THE DRAWINGS

[0016] The features and components of the following
figures are illustrated to emphasize the general principles of
the present disclosure. Corresponding features and compo-
nents throughout the figures can be designated by matching
reference characters for the sake of consistency and clarity.
[0017] FIGS. 1A-1E display onion-shaped crystal struc-
tures according to aspects of the present disclosure.

[0018] FIGS. 2A-2H display different stages of onion-
shaped crystal growth according to aspects of the present
disclosure.

[0019] FIGS. 3A-3B display topography of perpendicular
spiky crystal structures at varied calcium ion concentrations.
[0020] FIGS. 4A-4G display flower-shaped crystal struc-
tures according to aspects of the present disclosure.

[0021] FIGS. 5A-5D display crystal fusion inside poly-
peptide membranes according to the present disclosure.
[0022] FIGS. 6A-6D display mineralization (¢.g., crystal-
lization) occurring within thicker membrane cross-sections
according to the present disclosure.

[0023] FIGS. 7A-7B displays a use of compositions dis-
closed herein to regenerate bone tissue according to the
present disclosure.

[0024] FIGS. 8A-8D display characterizations of re-min-
eralized underlying crystal structures according to the pres-
ent disclosure.

[0025] FIGS. 9A-9B display mineralization on nylon
(FIG. 9A) and titanium (FIG. 9B) scaffolds according to the
present disclosure.

[0026] FIGS. 10A-10D display underlying mechanisms in
pathologies compared to mineralizing systems disclosed
herein.

[0027] FIGS. 11A-11I display positive effects of cells
growing on membranes in vitro according to the present
disclosure.

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US 2024/0301032 Al

[0028] FIGS. 12A-12F display characteristics of cells
growing on membranes in vitro according to the present
disclosure.

[0029] FIGS. 13A-13L display positive effects of cells
growing on membranes in vitro according to the present
disclosure.

[0030] FIGS. 14A-14D display characteristics of cells
growing on membranes in vitro according to the present
disclosure.

[0031] FIGS. 15A-15C display images of in vivo bone
regeneration performed on rabbits according to the present
disclosure.

[0032] FIGS. 16A-16D display characteristics of in vivo
bone regeneration performed on rabbits according to the
present disclosure.

[0033] FIGS. 17A-17F display images of in vivo bone
regeneration performed on rabbits according to the present
disclosure.

[0034] FIGS. 18A-18D display characteristics of in vivo
bone regeneration performed on rabbits according to the
present disclosure.

[0035] FIGS. 19A-19E display polarized microscopy of
crosslinked elastin (FIGS. 19A and 19B). SEM images of
membranes before mineralization of elastin (FIG. 19C).
Spherulites are revealed by SEM formed on elastin mem-
brane (FIGS. 19D and 19E) for 8 days.

[0036] FIGS. 20A-20F display SEM images of natural
elastin (FIGS. 20A and 20B) and natural collagen (FIGS.
20C and 20D) in bovine heart aorta showing elastin
entangled long filaments and collagen fibrils with visible
trile helix unit, respectively. TEM images of aorta showing
both elastin and collagen organization (FIG. 20E) across the
tissue, which in higher magnification collagen fibrils are
showing the gap-zone (FIG. 20F).

[0037] FIGS. 21A-21DD display histological analysis of
aorta and mitral valve before and after enzymatic digestion.
[0038] FIGS. 22A-22J display tissue samples from aorta
according to the present disclosure.

[0039] FIGS. 23A-23M display structural analysis of min-
eralization on aorta and mitral valve tissues after 8 days
mineralization

DETAILED DESCRIPTION OF THE
INVENTION

[0040] The present disclosure can be understood more
readily by reference to the following detailed description,
examples, drawings, and claims, and their previous and
following description. However, before the present compo-
sitions, systems, and/or methods are disclosed and
described, it is to be understood that this disclosure is not
limited to the specific devices, systems, and/or methods
disclosed unless otherwise specified, as such can, of course,
vary. It is also to be understood that the terminology used
herein is for the purpose of describing particular aspects
only and is not intended to be limiting.

I. Definitions

[0041] Unless defined otherwise, all technical and scien-
tific terms used herein have the same meaning as commonly
understood by one of ordinary skill in the art to which this
disclosure belongs. Although any compositions, methods
and materials similar or equivalent to those described herein

Sep. 12, 2024

can be used in the practice or testing of the present disclo-
sure. All publications mentioned are incorporated herein by
reference in their entirety.

[0042] The use of the terms “a,” “an,” “the,” and similar
referents in the context of describing the presently claimed
invention (especially in the context of the claims) are to be
construed to cover both the singular and the plural, unless
otherwise indicated herein or clearly contradicted by con-
text.

[0043] Recitation of ranges of values herein are merely
intended to serve as a shorthand method of referring indi-
vidually to each separate value falling within the range,
unless otherwise indicated herein, and each separate value is
incorporated into the specification as if it were individually
recited herein.

[0044] Use of the term “about” is intended to describe
values either above or below the stated value in a range of
approx. +/-10%; in other embodiments the values may
range in value either above or below the stated value in a
range of approx. +/-5%; in other embodiments the values
may range in value either above or below the stated value in
a range of approx. +/-2%:; in other embodiments the values
may range in value either above or below the stated value in
a range of approx. +/-1%. The preceding ranges are
intended to be made clear by context, and no further
limitation is implied. All methods described herein can be
performed in any suitable order unless otherwise indicated
herein or otherwise clearly contradicted by context. The use
of any and all examples, or exemplary language (e.g., “such
as”) provided herein, is intended merely to better illuminate
the disclosure and does not pose a limitation on the scope of
the disclosure unless otherwise claimed. No language in the
specification should be construed as indicating any non-
claimed element as essential to the practice of the disclosure.
[0045] As used herein, “amino acids” are organic com-
pounds that contains both amino and carboxylic acid func-
tional groups and serve as the building blocks for polypep-
tide or protein molecules.

[0046] As used herein, a “polypeptide” is a linear organic
polymer consisting ofa large number of amino-acid residues
bonded together in a chain, forming part of (or the whole of)
a protein molecule.

[0047] Other terms known in the art relating to the present
disclosure exist and are to be understood as used in the art,
unless otherwise specified.

II. Polypeptide Substrates

[0048] The present disclosure relates to polypeptide sub-
strates. Such substrates further comprise calcium ions,
wherein calcium ions are embedded within the substrates.
Additional ions and particles are also useful when embedded
in substrates including but not limited to hydroxyapatite
nanoparticles, fluoride ions, zinc oxide ions, and others.
Substrates include a variety of structures to be used in
numerous applications, disclosed herein. Substrates include
but are not limited to membranes, particles, coatings, slur-
ties, hydrogels, and the like which are conducive to crystal
growth. Particles include but are not limited to nanoparticles
and microparticles. Crystal growth is discussed herein. Crys-
tals can grow both from the inside and on the outside, or a
combination thereof, of substrates described herein.

[0049] The present disclosure relates to polypeptides used
in substrates. Polypeptides include but are not limited to
intrinsically disordered polypeptides and elastin-like poly-

Page 23

US 2024/0301032 Al

peptides (ELPs). Intrinsically disordered polypeptides
include but are not limited to elastin, resilin, amelogenin,
ameloblastin, and the like. Other exemplary polypeptides
include but are not limited to collagen, enamelin. Additional
exemplary polypeptides include but are not limited to any
polypeptide found in the enamel matrix. Though substrates
disclosed herein may be referred to as ELP substrates, it is
understood that the aforementioned additional polypeptides
are capable of being used, as well. As used herein, ELP may
comprise elastin-like recombinamers (ELRs).

[0050] The present disclosure relates to embedded cal-
cium ions within polypeptide substrates. Embedding cal-
cium ions alters the secondary structure of the substrates and
creates nucleation points inside the substrates. The creation
of nucleation points allows for specifically tailoring crystal
growth morphology and function, as described herein. Addi-
tional exemplary secondary structure alterations include but
are not limited to changes in secondary structures, amyloid
and amyloid-like formations, changes in mechanical char-
acteristics including stiffness, altered crosslinking, changes
in swelling capacity, and the like. (Elsharkawy, S., et al.,
Nature Communications, 9(2145): 1-12 (2018)). Benefi-
cially, this opens up the possibility for formation of crystals
both inside and outside the substrate.

[0051] Additionally, the incorporation of calcium ions
within the polypeptide substrate allows the formation of
novel crystal structures, together with crystal structures
possessing improved mechanical properties and improved
integration with bone and underlying crystal structures
including but not limited to dental enamel. Underlying
crystal structures refers to any pre-existing crystal structure
with which crystals can be integrated with using methods
and embodiments disclosed herein. Moreover, surprisingly,
the inventors discovered that crystal structures formed from
polypeptide substrate comprising calcium ions embedded
within the substrate have similar mechanical characteristics
including stiffness to natural dental enamel. FIGS. 7A-7B
displays use of compositions of the present disclosure for
bone regeneration.

[0052] FIGS. 8A-8D further display physical character-
ization of integration of compositions disclosed herein with
underlying crystal structures. FIG. 8A shows an SEM micro-
graph of re-mineralized enamel prism. FIG. 8B shows EDX
analysis confirmed formation of fluoride substituted apatite
(fluorapatite, FAp) nanocrystals crystals on top of native
hydroxyapatite crystals. FIG. 8C shows XRD characteriza-
tion showing formation of fluorapatite crystalline phase with
the formation of typical phosphate peaks at 604 and 565
cm”! (v,(PO,)) and 1035 cm”! v,(PO,), indicating apatite
formation.

[0053] As a non-limiting example, ELP molecules are
known to form amyloid-like ensembles with moderate levels
of B conformation including B-sheets and B-turns. Moderate
levels include levels of about 40% [ conformation. The
novel addition of embedded calcium ions in polypeptide
substrates enhances the formation of amyloid-like
ensembles. 8 conformation has been shown to be increased
up to about 80%

[0054] In a number of applications, amyloid-like
ensembles are highly desired. As a non-limiting example,
amyloid-like ensembles are desired for biomineralization of
underlying crystal structures including but not limited to
bone structures and dental enamel.

Sep. 12, 2024

[0055] The percentage of ELP in the substrate may be at
least 1%, 2%, 3%, 4% or at least 5% by weight of the
polypeptide substrate. In some embodiments, the percentage
by weight of ELP in the substrate may be no more than 20%,
15%, 10%, or 8% by weight.

[0056] The percentage by weight of ELP in the substrate
may be from 1-20% by weight, 1-15% by weight, 1-10% by
weight. Most preferably, 5% by weight.

[0057] As a non-limiting example where calcium ions are
embedded in a polypeptide substrate, calcium ions may be
Ca”.

[0058] The calcium ions may be provided by any sub-
stance capable of donating calcium ions known in the art. As
non-limiting examples, calcium-ion-donating substances
include but are not limited to CaCl,-nH,O (where n=0, 1, 2,
4, and 6), calcium carbonate (CaCO,), calcium phosphates
(e.g., hydroxyapatite, octacalcium phosphate), calcium
nitrate, any calcium-based mineral, and the like. One of skill
in the art would be aware of additional, suitable substances
capable of donating Ca?* ions.

[0059] Preferably, the calcium ions are provided by com-
pounds selected from the group consisting of CaCl,).
[0060] The present disclosure relates to optimized calcium
ion concentrations by weight of the substrate. Overly
elevated calcium ion concentrations lead to increased min-
eralization on the surface of the substrate. This prevents
diffusion of calcium, phosphorus, and fluorine ions into the
substrate, thus reducing the number of crystal structures
forming inside the bulk of the substrate.

[0061] The calcium ions may be present in an amount of
at least 0.001%, 0.002%, 0.003%, 0.004%, 0.005%, 0.006%,
0.007%, 0.008%, 0.009%, 0.01%, 0.02%, 0.03%, 0.04%,
0.05%, 0.06%, 0.07%, 0.08%, 0.09%, 0.1%, 0.12%, 0.14%,
0.16%0.18%, 0.20%, 0.22%0.24%, 0.28%, or 0.30% by
weight of the substrate. In some embodiments, the calcium
ions may be present in an amount of no more than 1.5%,
1.4%, 13%, 1.2%, 1.1%, 1%, 0.9%, 0.8%, 0.7%, 0.6%, or
0.5% by weight of the substrate.

[0062] Preferably the calcium ions may be present in an
amount of 0.005-1.5%, 0.005-0.7% by weight of the sub-
strate, more preferably 0.001-0.5% by weight of the sub-
strate.

[0063] Surprisingly, it has been observed that the number
of crystal structures formed decreases with an increase in the
amount of calcium ions present by weight in the substrate.
Advantageously, this means that the inventors have found an
polypeptide substrate which can be used to tune the mor-
phology or organisation of any hierarchical crystal structure
formed from the substrate.

[0064] The ELP may include various sequences, such as
those referenced in U.S. application Ser. No. 17/588,579,
which is incorporated by reference herein for any and all
purposes.

[0065] As an example, the ELP includes a peptide
sequence selected from the group consisting of

(a)
MGSSHHHHHHSSGLVPRGSHMESLLP -

[VPGIGVPGIGVPGKGVPGIGVPGIGVPGIGVPGIGVPGKGVPGIGVPG
IGAVIGRGDSPASSVPGIGVPGIGVPGKGVPGIGVPGIGVPGIGVPGIG

VPGKGVPGIGVPGIG]6-V

Page 24

US 2024/0301032 Al

-continued

(b)
MESLLP-

VPGIGVPGIGVPGKGVPGIGVPGIGEEIQI GHIPREDVDYHLYPVPGIG
VPGIGVPGKGVPGIGVPGIGVGVAPGVGVAPGVGVAPG]10-V

fe)
MESLLP-VPGIG VPGIG VPGKG VPGIG VPGIG VPGIG VPG

GI VPGKG VPGIG VPGIG]12-V

(d)
MESLLP-[{ (VPGIG} 2VPGKG (VPGIG} 2) 2- DDDEEKFLRRIGR

F (G-VPGIG) 2VPGKG (VPGIG} 2} 2]3-V

fe)
MESLLP-[ ( (VPGIG) 2VPGKG (VPGIG} 2) 2- DDDEEKFLRRIGR

F (G- (VPGIG) 2VPGKG (VPGIG} 2} 2]3 - (VPAVG) 20-V

(£)

MESLLP-[( (VPGIG) 2VPGKG (VPGIG) 2) 2- DDDEEKFLRRIGR
FG- ( (VPGIG) 2VPGKG (VPGIG} 2) 2]3 - (VPAVG) 20-

[ ((VPGIG) 2VPGKG (VPGIG) 2) 2-DDDEEKFLRRIGRFG-

({ (VPGIG) 2VPGKG (VPGIG) 2} 2]3-V.
and

ig)
MESLLP- (VPGVG VPGVG VPGEG VPGVG VPGVG) 10-

(VPAVG} 40-V.

[0066] By way of non-limiting example, the ELP may be
or comprise a statherin-ELP. As another example, the ELP
may be or comprise i) a pentapeptide sequence selected from
the group consisting of Gly-X-X-X-X, X-Gly-X-X-X, X-X-
Gly-X-X, X-X-X-Gly-X and X-X-X-X-Gly, (GXXXX,
XGXXX, XXGXX, XXXGX, XXXXG), wherein X is any
amino acid apart from proline, (ii) RGDS-ELP, and/or (iii)
Statherin-ELP. As a further example, the ELP may consist of
or comprise the sequence
MGSSHHHHHHSSGLVPRGSHMESLLP-[((VPGIG)
2VPGKG(VPGIG)2)2-DDDEEKFLRRIGRFG-((VPGIG)
2VPGKG(VPGIG)2)2)3-V.

[0067] The ELP may comprise a pentapeptide selected
from the group consisting of Gly-X-X-X-X, X-Gly-X-X-X,
X-X-Gly-X-X, | X-X-X-Gly-X and = X-X-X-X-Gly,
(GXXXX, XGXXX, XXGXX, XXXGX, XXXXG),
wherein X is any amino acid apart from proline. Preferably,
X is an amino acid selected from the group consisting of V,
P, G, S, F and I.

[0068] The ELP may comprise the tropoelastin recurrent
motif Val-Pro-Gly-X-Gly (VPGXG), where X is any amino
acid apart from proline.

[0069] The ELP may comprises the tropoelastin recurrent
motif Pro-Gly-Ile-Pro-Gly (PGIPG).

[0070] The ELP may comprise the tropoelastin recurrent
motif Pro-Val-Gly-Ser-Gly (PVGSG).

[0071] The ELP may comprise the tropoelastin recurrent
motif Val-Gly-Phe-Pro-Gly (VGFPG).

[0072] Native elastin itself may also be used with recur-
rent motif Val-Pro-Gly-Val-Gly.

[0073] ELPs are recombinant proteins. They can be pro-
duced in bacterial cells or purchased.

Sep. 12, 2024

[0074] An exemplary polypeptide substrate disclosed
herein includes polypeptide membranes including ELP
membranes. Membranes disclosed herein may range from
about 1 micrometre to about 2000 micrometres in thickness.
In a preferred embodiment, membranes may range from
about 40 micrometre up to about 80 micrometres in thick-
ness.

[0075] In one embodiment, the ELP membrane may have
a thickness of from 0.5 mm-1.5 mm, 0.6 mm-1.4 mm,
0.7-1.3 mm, 0.8 mm-1.2 mm, or 0.9-1.1 mm.

[0076] By incorporating calcium ions inside the mem-
brane, the inventors surprisingly discovered that thicker
membranes were able to form crystal structures, as shown in
FIGS. 6A-6D. Moreover, the formed crystals possessed
increased thickness when compared with existing crystal
structures produced from existing membranes not compris-
ing calcium ions

[0077] The ELP membrane may be cross-linked by a
cross-linker. Cross-linkers bind polypeptide molecules both
intramolecularly and intermolecularly. This function assists
in the formation of stable amyloid-like polypeptide
ensembles.

[0078] A cross-linker is an inorganic or organic reagent
that reacts with either a carboxylic group or an amine group
of a polypeptide substrate through covalent bonds, or non-
covalent bonds such as electrostatic, hydrogen bonds, or Van
der Waals. The polypeptide substrate may be cross-linked by
chemical cross-linking, enzymatic cross-linking by tissue
transglutaminase, photoinitiated and/or y-irradiation cross-
linking.

[0079] Preferably, cross-linker is hexamethyl diisocya-
nate. Additional cross-linkers include but are not limited to
glutaraldehyde, sodium tripolyphosphate, Riboflavin, phos-
phated riboflavin, 4 arm polyethylene glycol (PEG), succin-
imidyl glutarate, and PEG (Succinimidyl Carboxymethyl
Ester)2.

[0080] The polypeptide substrate may further comprise
collagen, amelogenin, bone sialoprotein, enamelin or phos-
phorylated serine. The polypeptide substrate may comprise
graphene, carbon nanotubules, and/or quantum dots. The
polypeptide substrate may comprise sugar, proteins, inor-
ganic particles and/or peptides. The skilled person would
also understand that a wide range of solvent soluble mate-
rials can be incorporated into the polypeptide substrate.
[0081] The polypeptide substrate may be biocompatible.
By “biocompatible” it is meant that the substrate is not
harmful or toxic to living tissue.

[0082] The polypeptide substrate may have a f-spiral
conformation. The presence of a B-spiral conformation can
be confirmed using circular dichroism (CD) and Fourier
transform infrared (FTIR) spectroscopy.

IL. Methods of Polypeptide Substrate Synthesis

[0083] The present disclosure relates to a method of
synthesis for forming polypeptide substrates. Various types
of substrates may be synthesized including membranes,
coatings, particles, hydrogels, and the like. Particles include
but are not limited to nanoparticles and microparticles.
Substrates described herein can be formed with an elastin-
like polypeptide (ELP) or any polypeptide disclosed herein.
ELP solutions described below can be prepared with any
polypeptide disclosed herein in order to form various poly-
peptide substrates.

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US 2024/0301032 Al

[0084] As a non-limiting example, the present disclosure
relates to forming ELP membranes, the process comprising
the steps of:

[0085] a) mixing an elastin-like polypeptide with a
source of calcium ions and a solvent to form an ELP
solution; and

[0086] b) applying the solution onto a surface to form a
membrane.

[0087] Step b) may comprise drop casting the solution
onto a surface.

[0088] The ELP may be present in an amount of at least
1%, 2%, 3%, 4% or at least 5% by volume of the ELP
solution. In one embodiment, the ELP may be present in an
amount of no more than 20%, 15%, 10%, or 8% of the ELP
solution.

[0089] The ELP may be present in an amount of from
1-20%, 1-15%, or 1-10% by volume of the ELP solution.
Most preferably, the ELP is present in an amount of 15% by
volume of the ELP solution.

[0090] The source of calcium ions may be any substance
capable of donating calcium ions known in the art. Exem-
plary calcium sources are described herein. The skilled
person would be aware of additional, suitable substances
capable of donating calcium ions.

[0091] Preferably, the calcium ions are Ca?*.

[0092] The calcium ions may be provided by any sub-
stance capable of donating calcium ions known in the art. As
non-limiting examples, calcium-ion-donating substances
include but are not limited to CaCl,) nH,O (where n=0, 1,
2, 4, and 6), calcium carbonate (CaCO ), calcium phos-
phates (e.g., hydroxyapatite, octacalcium phosphate), cal-
cium nitrate, any calcium-based mineral, and the like. One
of skill in the art would be aware of additional, suitable
substances capable of donating Ca** ions.

[0093] The source of calcium ions may be present in an
amount of at least 0.001%, 0.002%, 0.003%, 0.004%,
0.005%, 0.006%, 0.007%, 0.008%, 0.009%, 0.01%, 0.02%,
0.03%, 0.04%, 0.05%, 0.06%, 0.07%, 0.08%, 0.09%, 0.1%,
0.12%, 0.14%,0.16%0.18%, 0.20%, 0.22%0.24%, 0.28%, or
0.30% by volume of the ELP solution. In one embodiment,
the source of calcium ions may be present in an amount of
no more than 1.5%, 1.4%, 1.3%, 1.2%, 1.1%, 1%, 0.9%,
0.8%, 0.7%, 0.6%, or 0.5% of the ELP solution by volume.
[0094] Preferably the source of calcium ions may be
present in an amount of 0.005-1.5% by volume or 0.005-0.
7% by volume of the ELP solution, more preferably 0.001-
0.5% by volume of the ELP solution.

[0095] ELP may be present in 5% w/v of the ELP solution.
Additional, non-limiting examples include ELP present in
about 0.1% w/v up to about 20% w/v, about 1% w/v up to
about 19% w/v, about 2% w/v up to about 18% w/v, about
3% w/v up to about 17% w/v, about 4% w/v up to about 16%
wiv, about 5% w/v up to about 15% w/v, about 6% w/v up
to about 14% w/v, about 7% w/v up to about 13% w/v, about
8% wiv up to about 12% w/v, and about 9% w/v up to about
11% w/v of the ELP solution.

[0096] The solvent may be any solvent suitable for dis-
solving ELP. Such solvents would be well known to the
person skilled in the art. Non-limiting examples of solvents
include but are not limited to 100% water, ethanol mixtures,
ethanol-water mixtures, dimethylformamide (DMF), dim-
ethyl sulfoxide (DMSO), and the like. Additional exemplary
solvents include phosphate buffer saline (PBS) solution.

Sep. 12, 2024

Such a solvent has been shown to be able to be used with
beta-[tris(hydroxymethyl)phosphino]propionic acid (THPP)
as a crosslinker.

[0097] Preferably, the solvent is dimethylformamide
(DMF) and/or dimethyl] sulfoxide (DMSO).

[0098] The step b) of applying the solution onto a surface
may comprise the steps of dropping the solution onto the
surface and evaporating the solvents.

[0099] The surface may be any surface suitable for receiv-
ing the ELP solution. Such surfaces would be well known to
the skilled person.

[0100] Preferably, the surface is a polymeric material.
[0101] Preferably, the surface is poly(dimethylsiloxane)
(PDMS). Any surface known in the art may be used,
however.

[0102] The step a) may further comprise the step of
mixing the ELP solution with a cross linker, which cross-
linker may be in solution.

[0103] Preferably, the cross-linker is hexamethy] diisocya-
nate. Additional exemplary crosslinkers are disclosed
herein.

[0104] As a non-limiting example, one synthetic process
for creating an ELP membrane includes a first step of
dissolving ELP molecules into a mixture of anhydrous
dimethy formamide (DMF) and dimethyl] sulfoxide (DMSO)
solvents at a 9:1 ratio. Such solution is then mixed with
CaCl,-2H,0 at a range of concentrations from about 0.01%
up to about 0.5% w/v at room temperature inside a humidity
controlled (e.g., <20% humidity) glovebox. The ELP-Ca
solution can then be crosslinked with hexamethylene diiso-
cyanate (HDI) or glutaraldehyde at about 0.5% up to about
5% viv before being drop-casted on top of a polydimethyl-
siloxane (PDMS) surface and dried overnight.

IV. Crystal Formations

[0105] The present disclosure relates to crystal formations
growing in combination with polypeptide substrates
described herein. Crystal formations include but are not
limited to nanocrystals. Crystal formations can grow in a
variety of ways with relation to a polypeptide substrate. As
a non-limiting example, crystals can grow where the nucle-
ation only takes place within the substrate. The incorpora-
tion of ions, including calcium ions, into the polypeptide
substrate, also allows for crystals to be grown by nucleation
both inside and outside the substrate. As a non-limiting
example epitaxial growth of crystals at an underlying crys-
tal-ELP coating interface occurred by growing crystals
inside the polypeptide substrate and towards the substrate
surface. This can lead to remineralization. Underlying crys-
tals include but are not limited to bone tissue and dental
enamel.

[0106] The crystal may be apatite. ELP-mediated apatite
nanocrystals exhibit similar physical and chemical proper-
ties as that of enamel and bone crystals. Apatite crystals
additionally grow epitaxially on underlying crystal struc-
tures including but not limited to bone tissue and dental
enamel and bone to recreate their native microstructure.
[0107] Apatite refers to a phosphate mineral. Apatites are
flexible structures with wide range of optional substitutions
that can happen in their lattice at both cation and anion
positions. Apatites have the general formula A,.(BOn),X,
(alternatively As(BOn),X). A may be a divalent cation
selected from the group consisting of Ca?*, Sr°*, Ba** and
Pb**. BOn is an anionic complex, such as an anionic

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US 2024/0301032 Al

complex selected from the group consisting of PO, ,
AsO,3-, VO,°> or CO,*-. X is generally an anion. Prefer-
ably, X is selected from the group consisting of OH, F and
Cl.

[0108] Apatites have hexagonal crystallographic symme-
try. Such geometry may additionally be described as hex-
agonal flat ended geometry. The space group of apatites is
usually (P63/m) where the 6-fold c-axis is perpendicular to
3 a-axes at 120° to one another with some lower symmetry
analogues.

[0109] The apatite may be selected from the group com-
prising fluroapatite, hydroxyapatite and chlorapatite.
[0110] Preferably, the apatite is fluorapatite. Fluroapatite
is a phosphate mineral with the general formula Ca;(PO,),F.
Fluroapatite is alternatively referred to as Ca,o(PO,)F, or
FAp.

[0111] The apatite may be hydroxyapatite. Hydroxyapatite
is a phosphate mineral with the general formula Ca,(PO,)
3(OH).

[0112] The crystal may be located at least partly inside the
bulk of the polypeptide substrate. The crystals may be
located at least partly outside the bulk of the polypeptide
substrate.

[0113] The crystal may be located on the polypeptide
substrate surface.

[0114] The crystal may be located partly inside the bulk of
the polypeptide substrate and partly outside the bulk of the
polypeptide substrate.

[0115] The crystal may be located partly inside the bulk of
the polypeptide substrate and partly on the surface of the
polypeptide substrate.

[0116] The crystal may have a hierarchical structure.
[0117] By “hierarchical structure” it is meant a structure
having different structures at different length scales. Hier-
archy is a structural feature observed in natural tissues
including but not limited to enamel, nacre, and bone. Hier-
archy is difficult to achieve synthetically.

[0118] The present disclosure relates to growing structures
with different shapes inside the bulk of a substrate in a
tailored fashion. This allows for the formation of differently
organised hierarchically mineralized structures. Specifically
tailoring hierarchy allows fusing of crystals, as described
herein. This facilitates “controlled fusions” where a bundle
of nanocrystals fuses into a single large crystal. Tailored
hierarchy allows for control and limiting capabilities con-
cerning the extent of fusion.

[0119] The crystal may comprise nanostructures, micro-
structures and macrostructures assembled in a hierarchal
order across multiple length-scales. The length-scales can be
crystallographic, nanometre, micrometre, one hundred
micrometre and millimetre. Preferably, each level of hier-
archy comprises morphologically distinct structures.

[0120] At the crystallographic length-scale, the material
may be apatite.

[0121] In growth from underlying crystal structures, hex-
agonal apatite nanocrystals were observed to grow epitaxi-
ally from the underlying crystal structure-ELP interface
outwards through the ELP matrix. Underlying crystal struc-
tures include but are not limited to bone tissue and dental
enamel. In this case, the growth is regulated and limited by
the thickness of the ELP matrix, generating apatite layer
similar to the thickness of the ELP coating.

[0122] At the nanometre length scale the structures of the
invention may comprise nanocrystals.

Sep. 12, 2024

[0123] Crystals disclosed herein may be antimicrobial in
nature. The term ‘antimicrobial’ generally refers to sub-
stances or components that can kill, or inhibit the growth of,
microorganisms. As a non-limiting example, spiky nanoc-
rystals described further below grow perpendicular to a
substrate and disrupt bacterial membranes when bacteria
come in contact to the substrate, thus exhibiting antibacterial
properties.

A. Onion-Like Nanocrystal Formations

[0124] The nanocrystals may be arranged in “onion-like”,
formations in that layers of crystals are superposed, as
shown in FIGS. 1A-1E. Onion-like growth patterns include
hexagonal nanocrystals nucleating, growing, and organizing
into dumbbell-shaped structures to form the inner most layer
of the onion. This is followed by deposition of multiple
layers of nanocrystals on top of each other. Stages of
onion-shaped growth patterns are shown in FIGS. 2A-2H.
Onion-like growth differs from previous methods of crystal
growth including concentric ring growth where apatite
nanocrystals nucleate within the bulk of an ELP matrix to
form the root of a mineralized structure. Nanocrystals from
this concentric ring root grow, emerge, and spread radially
on the surface of the substrate. When the aligned nanocrys-
tals emerged out of the bulk and onto the substrate surface,
they organized into microscopic circular concentric rings,
different from onion-like growth patterns.

[0125] Each adjacent layer of nanocrystals may be sepa-
rated by a layer of ELP. Various layers of ELP and nanoc-
rystals can be formed by replenishing mineralizing solution
during crystal formation. As a non-limiting example, min-
eralizing solution can be replenished every 2 days, as it was
observed that the pH of the solution falls from 6 to 4 every
2 days. Replenishing the mineralizing solution results in
nucleation and growth of new layers of crystals on top of
previous layers. This process is described further below.
[0126] The number of layers of nanocrystals may decrease
as the percentage by weight of calcium ions incorporated
into a polypeptide substrate increases.

[0127] The layers of onion-like nanocrystals may be
located inside the bulk of the substrate.

[0128] The onions structures are visible on micro-scale. At
nanoscale they are composed of hexagonal apatite nanoc-
rystals.

[0129] The onion-like shaped nanocrystals comprise an
exemplary diameter of at least 10 nm, 11 nm, 12 nm, 13 nm,
14 nm, 15 nm, 16 nm, 17 om, 18 nm, 19 nm, and 20 nm.
Diameters of onion-like nanocrystals are determined by the
length of the nanocrystals growing axially from the substrate
surface in onion-like “layers.” Diameters can be increased
by subjecting onion-like shaped nanocrystals to mineraliza-
tion solutions for longer periods, as disclosed herein. The
use of thicker substrates for growing onion-like shaped
nanocrystals can also increase the diameter.

[0130] The onion-like nanocrystals may create a mineral-
ized layer extending from the substrate surface with a
thickness of at least 1 jm, 5 um, 10 um, 15 pm, 20 wm, 25
tum and no more than 100 jum, 90 um, 80 um, 70 jum, 60 pm.
The thickness may be from 1-100 um, 10-90 tm, 20-80 um,
30-70 jum, 40-60 jum. The overall mineralized layer may be
composed of multiple individual layers of onion-like nanoc-
rystals. As a non-limiting example, a single layer of onion-
like nanocrystals may range from about | jum up to about 5

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US 2024/0301032 Al

um. By growing multiple such layers on top of each other,
thicknesses disclosed above are achieved.

B. Needle-Like or Spiky Nanocrystal Formations

[0131] Crystal formations may comprise one or more
needle shaped or “spiky” nanocrystals, as shown in FIGS.
3A-3B. The crystals may comprise a plurality of needle
shaped nanocrystals. Needle shaped or “spiky” nanocrystals
grow to form the thick mineralized layer on top of a
substrate. The needle shaped nanocrystals may be located on
the polypeptide substrate surface.

[0132] The needle shaped nanocrystals may be orientated
perpendicular to the substrate surface.

[0133] In one embodiment, the needle shaped nanocrystals
extend axially from the substrate surface.

[0134] The needle shaped nanocrystals may grow from the
surface of the substrate.

[0135] The needle shaped nanocrystals comprise an exem-
plary diameter of at least 50 nm, 55 nm, 60 nm, 65 nm, 70
om, 75 om, 80 nm, 85 nm, 90 nm, 95 nm, and 100 nm.
[0136] The needle shaped nanocrystals may create a min-
eralized layer extending from the substrate surface with a
thickness of at least 1 um, 5 um, 10 wm, 15 pum, 20 pm, 25
uum and no more than 100 pm, 90 jum, 80 jum, 70 pum, 60 um.
The thickness may be from 1-100 um, 10-90 jum, 20-80 um,
30-70 \um, 40-60 jm. Preferably, the needle shaped nanoc-
rystal layer may have a thickness of 50 um. Thickness of the
layer created by needle shaped nanocrystals is determined
by the length of the nanocrystals growing axially from the
substrate surface. The overall mineralized layer may be
composed of multiple individual layers of needle shaped
nanocrystals. As a non-limiting example, a single layer of
needle shaped nanocrystals may range from about 5 um up
to about 10 um. By growing multiple such layers on top of
each other, thicknesses disclosed above are achieved.
[0137] Beneficially, these structures have been observed to
have improved mechanical characteristics including stiff-
ness. The generated layer of mineralized spiky layer is
capable of being exposed without a ELP layer cover, due to
the spiky layer’s improved mechanical characteristics
including stiffness.

C, Flower-Like Nanocrystal Formations

[0138] Alternatively, the crystal structure may comprise a
flower-like shaped nanocrystal, as shown in FIGS. 4A-4G.
Flower-like formations include bundles of hexagonal nanoc-
rystal that grow together forming a prisms or structures
similar to the “petals” of flower.

[0139] The flower-liked shaped nanocrystal may be
located on the inside of the bulk of the polypeptide substrate.
[0140] Surprisingly, the inventors observed that the num-
ber of flower-liked shaped nanocrystals decreased as the
percentage by weight of calcium ions incorporated into the
polypeptide substrate of the present invention increased.
[0141] Surprisingly, it was observed that when flower-
liked shaped nanocrystals were formed on the inside of the
polypeptide substrate, needle shaped nanocrystals did not
form on the exterior of the polypeptide substrate.

[0142] This demonstrates that hierarchical growth of crys-
tals can be controlled by the use of a polypeptide substrate
according to the present disclosure.

[0143] The nanocrystals within the substrate may be
fused, as shown in FIGS. 5A-5D. Fusing can be achieved by

Sep. 12, 2024

mineralizing already mineralized structures (e.g., flower-
like) at lower pH values (e.g., at a pH of about 4). It is
additionally possible to incur fusing at pH’s of about 5. At
these lower pHs, mineralized structures have been shown to
fuse.

[0144] Surprisingly, the inventors observed that fused
crystals have improved mechanical properties and are able
to fuse and better integrate with mineralized tissues.
[0145] The flower-like shaped nanocrystals comprise an
exemplary diameter of at least 30 nm, 31 nm, 32 nm, 33 nm,
34 nm, and 35 nm. Diameters of flower-like nanocrystals are
determined by the nanocrystals growing axially from the
substrate surface in “petals.” Diameters can be increased by
subjecting flower-like shaped nanocrystals to mineralization
solutions for longer periods, as disclosed herein. The use of
thicker substrates for growing flower-like shaped nanocrys-
tals can also increase the diameter.

[0146] The flower-like nanocrystals may create a miner-
alized layer extending from the substrate surface with a
thickness of at least 1 wm, 5 um, 10 um, 15 pm, 20 wm, 25
tum and no more than 100 jum, 90 um, 80 pm, 70 pm, 60 pm.
The thickness may be from 1-100 um, 10-90 jum, 20-80 jm,
30-70 jum, 40-60 jum. The overall mineralized layer may be
composed of multiple individual layers of flower-like nanoc-
rystals. As a non-limiting example, a single layer of flower-
like nanocrystals may range from about 2 um up to about 20
um. By growing multiple such layers on top of each other,
thicknesses disclosed above are achieved.

[0147] The inventors observed that thicker crystals may
develop inside ELP membranes having a thickness of from
0.5 mm-1.5 mm, 0.6 mm-1.4 mm, 0.7-1.3 mm, 0.8 mm-1.2
mm, or 0.9-1.1 mm.

[0148] The crystal may be antimicrobial. The term ‘anti-
microbial’ generally refers to substances or components that
can kill, or inhibit the growth of, microorganisms.

V. Methods of Crystal Formation Synthesis

[0149] The present disclosure relates to methods of crystal
formation synthesis. Crystals can be grown on the surface or
from within the polypeptide substrates disclosed herein. As
a non-limiting example, crystal formation synthesis may
comprise the steps of contacting a substrate with a miner-
alizing solution. Crystal formation synthesis processes dis-
closed herein are applicable with any substrate disclosed
herein. Membranes may serve as non-limiting examples in
the foregoing disclosure. Additionally, elastin-like polypep-
tides may serve as non-limiting examples of polypeptides to
be used for substrates below. It is to be understood any
proteins disclosed herein can be used in the polypeptide
substrates compatible for crystal growth.

[0150] The step of contacting the substrate may comprise
submerging and/or incubating the substrate in the mineral-
izing solution. The step of incubating comprises nucleation
followed by crystal growth.

[0151] The mineralizing solution may comprise PO,*
ions. As additional, non-limiting examples, mineralized
structures can be grown using magnesium ions, calcium
ions, phosphorus, and fluorine ions. In uses of magnesium
ions, energy-dispersive x-ray spectroscopy (EDX) has
shown that mineralized structures exhibited the presence of
Mg indicating the incorporation of Mg ions into the crystal
lattice.

[0152] The mineralizing solution may comprise at least
0.1 mM, 0.2 mM, 0.3 mM, 0.4 mM, 0.5 mM, 0.6 mM, 0.7

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US 2024/0301032 Al

mM, 0.8 mM, 0.9 mM, 1 mM PO,>- ions. In some embodi-
ments, the mineralizing solution may comprise no more than
5 mM, 4.5 mM, 4.0 mM, 3.5 mM, 3.0 mM, 2.5 mM, or 2.0
mM PO,*.

[0153] The mineralizing solution may comprise 0.1
mM-3.5 mM, 0.1 mM-3 mM, 0.1-2.5 mM, 0.2 mM-2.5 mM,
0).3-2.5 mM, 0.4-2.5 mM, 0.5-2.5 mM, 0.6-2.5 mM, 0.7-2.5
mM, 0.8-2.5 mM, 0.9-2.5 mM, 1-2.5 mM, 1.1-2.5 mM,
1.2-2.5 mM, 1.3-2.5 mM, 1.4-2.5 mM, or 1.5 mM-2.5 mM
PO,*-. Preferably, the mineralizing solution comprises 2
mM PO,*.

[0154] The PO,*- ions may be provided by any substance
capable of donating PO," ions.

[0155] Preferably, the PO,,°~ ions are provided by calcium
phosphate. Varying concentrations of calcium and phospho-
rus-based ions can be used in mineralizing solutions. In
some instances, even saliva with very low ion concentra-
tions can lead to mineralization. In such examples, an
underlying native surface for remineralization is required.
As a non-limiting example, a variety of underlying crystal
structures can serve as the underlying native service. Under-
lying crystal structures include but are not limited to bone
tissue and dental enamel. A first deposit of an ELP substrate
including a coating can then be deposited and mineralized
either by artificial saliva or by supersaturated mineralization
solution. This will create new apatite crystals growing
epitaxially from the underlying crystal structure-ELP inter-
face outwards through the ELP matrix.

[0156] The mineralizing solution may comprise F~ ions.
[0157] The mineralizing solution may comprise at least
0.1 mM, 0.2 mM, 0.3 mM, 0.4 mM, 0.5 mM, 0.6 mM, 0.7
mM, 0.8 mM, 0.9 mM, 1 mM F° ions. In one embodiment,
the mineralizing solution may comprise no more than 5 mM,
4.5 mM, 4.0 mM, 3.5 mM, 3.0 mM, 2.5 mM, or 2.0 mM F~
ions.

[0158] The mineralizing solution may comprise 0.1
mM-3.5 mM, 0.1 mM-3 mM, 0.1-2.5 mM, 0.2 mM-2.5 mM,
0.3-2.5 mM, 0.4-2.5 mM, 0.5-2.5 mM, 0.6-2.5 mM, 0.7-2.5
mM, 0.8-2.5 mM, 0.9-2.5 mM, 1-2.5 mM, 1.1-2.5 mM,
1.2-2.5 mM, 1.3-2.5 mM, 1.4-2.5 mM, or 1.5 mM-2.5 mM
F” ions. Preferably, the mineralizing solution comprises 2
mM F ions.

[0159] The F~ ions may be provided by any substance
capable of donating F~ ions.

[0160] Preferably, the F~ ions are provided by sodium
fluoride. As additional, non-limiting examples, fluoride ions
can also be provided by stannous fluoride (SnF,) and sodium
monofiuorophosphate (Na,PO;F).

[0161] The mineralizing solution may comprise PO,?-
ions and F~ ions.

[0162] Preferably, the mineralizing solution comprises 2
mM calcium phosphate and 2 mM sodium fluoride.

[0163] Alternatively, the mineralising solution may com-
prise calcium phosphate and sodium fluoride in an amount
of from 0.1 mM-0.65 mM, 0.15-0.6 mM, 0.2-0.55 mM.
Preferably, 0.25 mM, or 0.5 mM.

[0164] In such an embodiment, the inventors discovered
that the combination of a thicker ELP membrane of around
1 mm and a concentration of calcium phosphate of around
0.1 mM-0.65 mM formed crystal structures inside the mem-
brane having increased thickness.

[0165] The contacting step, wherein the polypeptide sub-
strate comes into contact with a mineralizing solution, may
be carried out at physiological temperature.

Sep. 12, 2024

[0166] The contacting step may be carried out at a tem-
perature of about 35-38° C. Most preferably, about 37° C.
[0167] The contacting step may be carried out for a period
ofat least 8 hours, at least 10 hours, at least 12 hours, at least
1 day, 2 days, 3 days, 4 days or 5 days. In some embodi-
ments, the contacting step may be carried out for a period of
no more than 20, 15, 10, 9 or 8 days.

[0168] The contacting step may be carried out for 1-20
days, 5-15 days, 5-10 days. The length of such step may be
dependent upon the thickness of the desired substrate (e.g.,
membranes, particles, etc.). As a non-limiting example, a 50
tum thick membrane may require 7-10 days for an optimum
mineralization period for the membranes to mineralize.
[0169] The contacting step may be carried out at a pH of
at least 2, 3, 4, 5, or 6. In some embodiments, the contacting
step may be carried out at a pH of no more than 11, 10, 9,
or 8. The pH may be from 2-11, 3-8, 4-8, 4-7, or 5-7. Most
preferably the pH is 6.

[0170] The pH may change over time. For example, the
pH may decrease to around 4 after 2 days of incubation.
[0171] The present disclosure relates to methods of fusing
crystal structures. Fusing typically occurs at lower pH
values including but not limited to pH values of about 4 and
below. At such pH values, re-mineralization of previously
mineralized structures leads to fusion of adjacent crystals.
Fusing can occur at elevated pH values of about 5. This
produces increased thickness of individual crystals. Fusion
additionally leads to improved mechanical characteristics
including stiffness, cement-like characteristics, stability,
acid resistance, and the like.

[0172] In such an embodiment, the process may further
comprise the step of replacing the mineralizing solution. The
step of replacing the mineralizing solution may be carried
out after a period of 8 hours, 10 hours, 12 hours, 1 day, 2
days, 3 days, 4 days or 5 days of incubation. In doing so, the
resulting crystal structure has been observed to form con-
centric nanocrystals inside the ELP membrane and needle
shaped nanocrystals on the membrane surface as described
herein.

[0173] The process may further comprise the step of
maintaining the pH for the duration of the contacting step.
[0174] Preferably, the pH is maintained at pH 4-7, or 5-7,
most preferably 6.

[0175] The pH may be maintained by the addition of a
buffer solution.

[0176] The buffer solution may have a concentration of at
least 10 mM, 15 mM, 20 mM, 30 mM and no more than 60
mM, 55 mM, 50 mM, 45 mM, 40 mM. Preferably the buffer
solution has a concentration of from 25-45 mM, 30-40 mM.
Most preferably, 35 mM.

[0177] Preferably the buffer solution is a BIS-TRIS buffer.
[0178] Surprisingly, the inventors discovered that main-
taining the pH at 6 throughout the contact period results in
the formation of flower-shaped nanocrystals on the inside of
ELP membranes as described herein. More surprisingly, the
inventors discovered that maintaining the pH at around 6
prevented the formation of needle shaped nanocrystals on
the surface of the membrane, as described herein.

[0179] The process may further comprise the step of
contacting the membrane at a first pH and then contacting
the membrane at a second, lower pH. The first pH may be
5.5-6.5. The second lower pH may be from 3.0-4.0. Prefer-
ably, the first pH is around 6.0 and the second lower pH is
around 4,

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US 2024/0301032 Al

[0180] The membrane may be contacted at the first pH for
around 7-13 days, 8-12 days, 9-11 days. Most preferably 10
days. The membrane may be contacted at the second pH for
around 7-13 days, 8-12 days, 9-11 days. Most preferably 10
days.

[0181] In such an embodiment, it was observed that the
crystals fused as described in.

VI. Applications and Devices

[0182] The present disclosure relates to a variety of appli-
cations and devices of the polypeptide substrates comprising
crystal formations described herein. As non-limiting
examples, the present disclosure relates to applications and
devices of various polypeptide substrates including crystal
formations including but not limited to polypeptide par-
ticles, membranes, hydrogels, and the like including onion-
like, needle-like, flower-like and other such crystal forma-
tions disclosed herein. Such combinations of polypeptide
substrates and crystal formations can be used in coatings,
enamels, implants, pastes, spreads, slurries, and the like.
[0183] Combinations of polypeptide substrates compris-
ing crystal formations described herein can be used in
medicine, such as for use in the prevention and/or treatment
of demineralisation of teeth, dental disease, dental hyper-
sensitivity, bone demineralisation, low bone density, bone
disease, bone defects, osteoporosis, or cardiovascular dis-
ease, Such combinations can additionally be used to treat
diseases relating to calcification including diseases related to
tissue calcification. Combinations disclosed herein are also
useful for analysing and treating Alzheimer’s disease. The
present disclosure relates to the supramolecular organization
of organic molecules that form Maltese-like cross pattern
structures (organic spherulites). Such structures nucleate and
grow additional mineralized structures (inorganic spheru-
lites). Both of these organic and inorganic structures exhibit
similarity to structures seen in pathologies such as cardio-
vascular calcification and calcification associated with
Alzheimer’s disease (FIGS. 10A-10D). The structures dis-
closed herein may present a model for exploring and under-
standing mechanistic insights of associated tissue calcifica-
tion.

[0184] The present disclosure relates to a combination as
disclosed herein for use in the prevention and/or treatment of
bone demineralisation, low bone density, bone disease, bone
defects and/or osteoporosis. FIGS. 11A-18D display both in
vitro results (FIGS. 11A-14D) and in vivo results using
rabbits (FIGS. 15A4-18D) of using combinations disclosed
herein to treat bone defects. Combinations disclosed herein
can additionally be used in treating or preventing cardio-
vascular disease.

[0185] The present disclosure relates to a medical device
or pharmaceutical composition comprising a combination,
as disclosed herein. The medical device may be a medical
implant, synthetic graft, prosthesis, orthosis, paste, mal-
leable putty, film, or bone implant.

[0186] The present disclosure relates to a medical device
or pharmaceutical composition comprising a substrate, as
disclosed herein. The medical device may be a medical
implant, synthetic graft, prosthesis, orthosis, paste, mal-
leable putty, film, or bone implant.

[0187] The present disclosure relates to a crystal for use in
the prevention and/or treatment of demineralisation of teeth,
dental disease, dental hypersensitivity, bone demineralisa-

Sep. 12, 2024

tion, low bone density, bone disease, bone defects, osteo-
porosis, or cardiovascular disease.

[0188] The present disclosure relates to a substrate for use
in the prevention and/or treatment of demineralisation of
teeth, dental disease, dental hypersensitivity, bone deminer-
alisation, low bone density, bone disease, bone defects,
osteoporosis, or cardiovascular disease.

[0189] The present disclosure relates to a substrate as
described herein for use in a method of tissue regeneration,
the method comprising the steps of depositing the substrate
on the tissue and contacting the substrate with a mineral-
ization solution.

[0190] The tissue may be any tissue with an underlying
crystal structures, such as bone tissue.

[0191] Substrates including various crystal growths, as
disclosed herein, may be coated or partially coated on a
medical implant, synthetic graft, prosthesis, orthosis, paste,
hydrogel, malleable putty, film, three-dimensional printed
implants, or bone implant. The surface of the medical
implant, synthetic graft, prosthesis, orthosis, paste, mal-
leable putty, film, dental implant or bone implant may be
partially or fully covered with the crystal and/or substrate.
The coating can be chemically bonded to the surface through
a variety of mechanisms including but not limited to cova-
lent bonding, physisorption, and the like.

[0192] Ina further aspect of the present invention there is
provided a method of growing a crystal according to the
present disclosure on a medical implant, synthetic graft,
prosthesis, orthosis, paste, malleable putty or film, the
method comprising the steps of contacting a medical
implant, synthetic graft, prosthesis, orthosis, paste, mal-
leable putty or film comprising a substrate with a mineral-
izing solution as described herein. As such, the medical
device or material can grow various crystal structures from
the substrate contained therein.

VII. Methods of Use in Cardiovascular
Calcification

[0193] The present disclosure relates to uses of disclosed
compositions of polypeptide substrates and crystal forma-
tions to assess and treat tissue calcification. In particular, the
present disclosure relates to cardiovascular calcification.
Compositions disclosed herein help to illuminate the mecha-
nisms behind cardiovascular calcification. Though tradi-
tional mechanisms focus on cellular processes leading to or
controlling the unwanted mineralization on soft tissues,
extracellular components including elastin are fundamental
in regulating the mechanical properties of heart tissues.
[0194] The present disclosure relates to a toolkit to control
compositions of tissues by selective digestion of ECM
components. This can be used in designing disease-specific
in-vitro models, as disclosed herein. Systematic enzymatic
digestion of cardiovascular tissues illuminates elastin’s role
in cardiovascular calcification. Elastin’s degeneration dis-
plays evident changes in the structure and composition of
extracellular matrix (ECM) of heart tissue. As such, the
present disclosure relates to methods of treatment and pre-
vention of unwanted pathological disorders.

[0195] Human aorta is made from three layers known as
tunica adventitia, tunica media, and tunica intima, which are
all responsible for circulating oxygenated blood from the
heart throughout the whole body. Tsamis, A., J. R. Soc.
Interface 2013, 10 (83), 20121004; Komutrattananont, P., et
al., Anat. Cell Biol. 2019, 52 (2), 109-114. Within this

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10

microstructure of the aortic wall, elastin and collagen are the
main contributors to its elasticity and mechanical strength,
respectively. Berillis, P., Open Circ. Vasc. J. 2013, 6 (1).
Collagen is mainly located in the tunica adventitia (outer
layer) and tunica media (middle layer), while elastin is
mainly located in tunica media (middle layer). In cardio-
vascular diseases, inflammatory conditions can affect the
compliance of the aortic wall, which can be observed by
changes in the aorta’s diameter, length, and thickness,
whereas age-related changes cause enlargement and struc-
tural changes in tunica media. Komutrattananont, P., et al.,
Anat. Cell Biol. 2019, 52 (2), 109-114; Berillis, P., Open
Cire. Vase. J. 2013, 6 (1).

[0196] Collagen a component of the extracellular matrix
(ECM) of heart valves, providing stiffness, strength, and
stability of the valve’s cusps. Kodigepalli, K. M., et al., J.
Cardiovasc. Dev. Dis. 2020, 7 (4), 57. Elastic fibers, which
are mainly composed of elastin, are predominantly arranged
in the form of continuous sheets along the radial and
circumferential axes, which facilitate valve motion and bear
a substantial amount of load without deformation. Hinton,
R. B., et al, Annu. Rev. Physiol. 2011, 73, 29-46. In a
diseased environment, the cusp and leaflet of the valves
thickens as a result of changes in the organization of
collagen fibers and the emergence of calcification.

[0197] While molecular mechanism of pathological calci-
fication remains unclear, several studies have highlighted
events resembling those in bone formation. Kempf, H., et
al., Front. Cell Dev. Biol. 2021, 9; Tintut, Y., et al., Biomo-
lecules 2021, 11 (10), 1482. For instance, in vessel wall
calcification, some cellular processes resemble those of
developmental osteogenesis including competition between
mineralization inhibitors and promoters, osteoblastic differ-
entiation, expression of bone matrix proteins, and formation
of hydroxyapatite. Kapustin, A., Curr. Opin. Pharmacol.
2009, 9 (2), 84-89; Persy, V. P., et al., Kidney Int. 2011, 79
(5), 490-493; Herrmann, M., et al., PLOS One 2020, 15 (2),
0228503; Kaartinen, M. T., et al., J. Histochem. Cytochem.
2007, 55 (4), 375-386; Rajamannan, N. M., et al., Circula-
tion 2011, 124 (16), 1783. Moreover, studies have reported
the presence of calcifying osteoblast-like cells within human
aortic valve cell cultures in vitro. Yu, B., et al., Basic to
Transl. Sci. 2017, 2 (4), 358-371. Furthermore, calcified
particles have been linked to triggering osteoblastic differ-
entiation of mesenchymal stem cells linked to vascular
tissue, but the source of these calcified particles has not been
identified. Several studies have taken a materials science
approach to shine light on this mysterious process. Bertazzo,
S., et al., Nat. Mater. 2013, 12 (6), 576-583; Hutcheson, J.
D., et al., Nat. Mater. 2016, 15 (3), 335-343. In a pioneering
study, Stevens and colleagues used advanced nano-analyti-
cal microscopy techniques and found that the unset of
cardiovascular calcification is not associated to surface
precipitation of calcium phosphate, but rather a more com-
plex biomineralization process that occurs within the bulk of
the tissue. Radvar, E., et al., Adv. NanoBiomed Res. 2021,
1 (8), 2100042.

[0198] The ECM is of paramount importance in the for-
mation of calcified structures. Even in the absence of cells,
tissues can become calcified. Watson, K. E., et al., Arterio-
scler. Thromb. Vasc. Biol. 1998, 18 (12), 1964-1971. Col-
lagen is believed to be one of the main sources of extracel-
lular calcification in cardiovascular tissues in a process that
progresses slowly over years or decades, resulting in accu-

Sep. 12, 2024

mulation of collagen, calcification, and disruption of the
tissue microarchitecture. Ruiz, J. L., et al., Cardiovasc.
Pathol. 2015, 24 (4), 207-212. However, these studies have
focused on analyzing tissues at later stages of calcification
and have not addressed the initial events triggering this
process. In addition, mineral-associated vesicles (MVs)
from cells undergoing osteoblastic differentiation can nucle-
ate and grow hydroxyapatite crystals when bound to not
only collagen, but also other ECM components such gly-
cosaminoglycans (GAGs). Kapustin, A. N., et al., Cire. Res.
2011, 109 (1), el-e12. Similarly, the source of these MVs
has not been identified. Furthermore, the apparent partici-
pation of other ECM components in calcification confirms a
complex multifactorial calcification scenario, which under-
lines the importance of identifying the origins of the calci-
fication process.

[0199] Elastin is the predominant ECM component of
elastic fibers in cardiovascular connective tissues. Elastic
fibers possess a very low turnover rate and thus insult to
elastic tissue can result in either degradation due to chronic
loss or excess (detrimental) accumulation. Humphrey, J. D.,
et al., Nat. Rev. Mol. cell Biol. 2014, 15 (12), 802-812;
Bailey, E. L., et al., Atherosclerosis 2014, 237 (2), e4.
During the initial stages of cardiovascular calcification,
macrophage derived elastolytic enzymes and matrix metal-
loproteinases degrade elastin, resulting in the release of
soluble elastin-derived peptides that can promote osteogenic
differentiation and subsequent calcification. Bailey, M., Car-
diovasc. Pathol. 2004, 13 (3), 146-155; Green, E. M., et al.,
Interface Focus 2014, 4 (2), 20130058. Sakata et al. reported
that modification in the elastin content of aorta led to
calcification in the aortic media. Sakata, N., et al., Nephrol.
Dial. Transplant. 2003, 18 (8), 1601-1609. Also, in athero-
sclerotic aorta, both apatite and whitlockite-type minerals
are shown by Raman spectroscopy to localize in the tunica
media (the elastic layer) as reported by You et al. in 201727.
Moreover, it has been shown that elastin can be associated
to matrix vesicles and has a greater propensity for calcifi-
cation as a result of ageing and specific pathologies (REF).
The role of elastin in inducing mineralization is reported in
a few studies in vitro. Kapustin, A. N., et al., Circ. Res. 2011,
109 (1), el-el2; Parashar, A., et al., J. Struct. Biol. 2021, 213
(1), 107637. For example, Gourgas et al. reported the
deposition of globular calcium phosphate minerals on fibers
and filaments on elastin-like polypeptide (ELP) membranes.
Gourgas, O., et al., Biomacromolecules 2019, 20 (7), 2625-
2636. Furthermore, the present disclosure relates to meth-
odologies to engineer ELP-based membranes with tunable
ELP conformation and geometrical confinement to investi-
gate organic-inorganic interactions within bulk environ-
ments. Tejeda-Montes, E., et al., Acta Biomater. 2012, 8 (3),
998-1009; Tejeda-Montes, E., Biomaterials 2014, 35 (29),
8339-8347; Elsharkawy, S., et al., Nat. Commun. 2018, 9
(1), 2145; Deng, X., et al., Mater. Today Bio 2021, 11,
100119.

[0200] There is currently no definitive therapy to prevent
or treat cardiovascular calcification and the underlying
mechanisms triggering this condition are not fully under-
stood. The risk factors rare not consistently correlated,
leaving clinicians uncertain about the optimum management
for these patients34. Surgery is the only effective treatment
but could lead to damage of the aortic or mitral valves,
which would require surgical replacement of the valve. In
addition, bio-prosthetic valves still carry a high risk of

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11

calcification and operative mortality. As such, the present
disclosure relates to uses of compositions disclosed herein in
order to illuminate the role of elastin in cardiovascular
calcification, as well as treating and preventing such calci-
fication.

[0201] The present disclosure relates to a major role
played by elastin in the onset of calcification of cardiovas-
cular tissues. Furthermore, materials science techniques
known in the art are used to characterize aorta and mitral
valve tissues at multiple size-scales from the molecular scale
and found that elastin plays a bigger role sequestering Ca°*
ions and generating Ca**-based mineralized structures com-
pared to collagen. This demonstrates an enhanced propen-
sity to calcify.

[0202] The present disclosure relates to elastin degrada-
tion and accumulation leading to changes in the structure
and composition of the ECM and generating a supramo-
lecular framework that can promote mineralization. Despite
mounting evidence that elastin may be central to the onset
and progression of cardiovascular calcification, limited
attention has been given at understanding its contribution
from a structural standpoint and from the molecular scale.
The present disclosure relates to this critical role of elastin.

ASPECTS
[0203] The present disclosure is related to the following
aspects.
[0204] 1. A polypeptide substrate comprising calcium.

ions, wherein the calcium ions are embedded within the
polypeptide substrate.

[0205] 2. A substrate according to aspect 1 wherein the
calcium ions are Ca**.

[0206] 3. Asubstrate according to any preceding aspect,
wherein the calcium ions are provided by CaCl,).

[0207] 4. Asubstrate according to any preceding aspect,
wherein the calcium ions are present in an amount of at
least 0.001% by weight of the substrate.

[0208] 5. A substrate according to aspect 4, wherein the
calcium ions are present in an amount of at least
0.005-1.5% by weight of the substrate.

[0209] 6. Asubstrate according to any preceding aspect,
wherein the polypeptide is a pentapeptide Elastin-like-
polypeptide selected from the group consisting of Gly-
X-X-X-X, X-Gly-X-X-X, X-X-Gly-X-X, X-X-X-
Gly-X and X-X-X-X-Gly, (GXXXX, XGXXX,
XXGXX, XXXGX, XXXXG), wherein X is any amino
acid from apart proline or

MGSSHHHHHHSSGLVPRGSHMESLLP-
[({VPGIG) 2VPGKG (VPGIG) 2) 2-
DDDEEKFLRRIGRFG- ( (VPGIG} 2VPGKG (VPGIG} 2) 2]3-V.

[0210] 7. Asubstrate according to any preceding aspect,
wherein the polypeptide substrate has a thickness of
from 0.5 mm-1.5 mm.

[0211] 8. A process for forming an elastin-like polypep-
tide membrane according to any one of aspects 1 to 7,
the process comprising the steps of:

[0212] a) dissolving elastin-like polypeptides with a
source of calcium ions and a solvent to form an ELP
solution; and

Sep. 12, 2024

[0213] _b) applying the solution onto a surface to form a
membrane.

[0214] 9. A process according to aspect 8, wherein the
ELP is present in an amount of from 1-20% by weight
of the solution.

[0215] 10. Aprocess according to aspect 8 or 9, wherein
the source of calcium ions may be present in an amount
of 0.005-1.5% by volume of the solution.

[0216] 11. A process according to any one of aspects 8
to 10, wherein the step a) further comprises the step of
mixing the ELP solution with a cross-linker.

[0217] 12. Aprocess according to aspect 11, wherein the
cross-linker is hexamethy! diisocyanate.

[0218] 13. A crystal formed from and at least partly
embedded in a substrate according to any one of
aspects 1 to 7.

[0219] 14. Acrystal according to aspect 13, wherein the
crystal is located at least partly inside the bulk of the
polypeptide substrate.

[0220] 15. Acrystal according to aspect 13, wherein the
crystal is located partly inside the bulk of the polypep-
tide substrate and partly on the surface of the polypep-
tide substrate.

[0221] 16. Acrystal according to any one of aspects 13
to 15, wherein the crystal has a hierarchical structure.

[0222] 17. Acrystal according to any one of aspects 13
to 16, wherein the crystal comprises nanocrystals.

[0223] 18. Acrystal according to aspect 17, wherein the
nanocrystals are arranged in concentric layers.

[0224] 19. Acrystal according to aspect 17, wherein the
nanocrystals have a needle shape.

[0225] 20. Acrystal according to aspect 19, wherein the
needle shaped nanocrystals are located on the polypep-
tide substrate surface and orientated perpendicular to
the polypeptide substrate surface.

[0226] 21. Acrystal according to aspect 17, wherein the
nanocrystal have a flower-liked shaped.

[0227] 22. Acrystal according to any one of aspects 17
to 21, wherein the nanocrystals within the substrate are
fused.

[0228] 23. A process for producing a crystal according
to any one of aspects 13 to 22 comprising the steps of
contacting a substrate according to any one of aspects
1 to 8 with a mineralizing solution.

[0229] 24. A process according to aspect 23, wherein
the mineralizing solution comprises PO,°~ ions and F~
ions.

[0230] 25. A process according to aspect 24, wherein
the PO,*~ ions and F” ions may be present in a
concentration of | mM-3 mM.

[0231] 26. A process according to aspect 24, wherein
the PO,*- ions and F~ ions may be present in a
concentration of 0.1 mM-0.65 mM.

[0232] 27. A process according to any one of aspects 23
to 26, wherein the contacting step is carried out for a
period of 5-10 days.

[0233] 28. A process according to any one of aspects 23
to 27, wherein the pH of the contacting step is from 4-7.

[0234] 29. A process according to any one of aspects 23
to 28, further comprising the step of replacing the
mineralizing solution after 2 days of incubation.

[0235] 30. A process according to any one of aspects 23
to 29, further comprising the step of maintaining the pH

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US 2024/0301032 Al

for the duration of the contacting step, wherein pref-
erably the pH is maintained at pH 4-7.

[0236] 31. A process according to any one of aspects
23-27, further comprising the steps of contacting the
substrate at a first pH and then contacting the substrate
at a second, lower pH, wherein preferably the first pH
is from 5.5-6.5 and the second lower pH is from
3.0-4.0.

[0237] 32. A crystal according to any one of aspects
13-22 for use in medicine, such as for use in the
prevention and/or treatment of demineralisation of
teeth, dental disease, dental hypersensitivity, bone
demineralisation, low bone density, bone disease, bone
defects, osteoporosis, or cardiovascular disease.

[0238] 33. A medical device, such as a medical implant,
synthetic graft, coating, prosthesis, orthosis, paste, mal-
leable putty, film, bone implant, or pharmaceutical
composition, comprising a crystal according to any one
of aspects 13 to 22.

[0239] 34. Amembrane according to any one of aspects
1 to 7 for use in medicine, such as for use in the
prevention and/or treatment of demineralisation of
teeth, dental disease, dental hypersensitivity, bone
demineralisation, low bone density, bone disease, bone
defects, osteoporosis, or cardiovascular disease.

[0240] 35. A medical device, such as a medical implant,
synthetic graft, prosthesis, orthosis, paste, malleable
putty, film, bone implant, or pharmaceutical composi-
tion comprising a substrate according to any one of
aspects 1 to 7.

[0241] 36. A method of growing a crystal according to
any one of aspects 13 to 22 on a medical implant,
synthetic graft, prosthesis, orthosis, paste, malleable
putty or film, the method comprising contacting a
medical implant, synthetic grafi, prosthesis, orthosis,
paste, malleable putty or film comprising a substrate
according to any one of aspects 1 to 7 with a miner-
alizing solution.

[0242] 37. A hybrid organic-inorganic system compris-
ing:

[0243] ordered apatite crystalline structures,

[0244] wherein the ordered apatite crystalline structures
comprise at least one of onion-like, needle-like, flower-
like, and prism-like microstructures; and

[0245] a protein substrate capable of growing the
ordered apatite crystalline structures thereon or therein,

[0246] wherein the protein substrate comprises a poly-
peptide,

[0247] wherein the polypeptide comprises a pentapep-
tide elastin-like-polyptide (ELP) selected from the
group consisting of Gly-X-X-X-X, X-Gly-X-X-X,
X-X-Gly-X-X, X-X-X-Gly-X and X-X-X-X-Gly,
(GXXXX, XGXXX, XXGXX, XXXGX, XXXXG),
wherein X is any amino acid apart from proline,

[0248] wherein the protein substrate comprises an
amount of ions embedded in the protein substrate, and

[0249] wherein the ions embedded in the protein sub-
strate provide nucleation points to allow for selectively
tailoring the ordered apatite crystalline structures.

[0250] 38. A hybrid organic-inorganic system according,
to aspect 37, wherein the ions are selected from a group
consisting of calcium ions, fluoride ions, and zine oxide
ions.

Sep. 12, 2024

[0251] 39. A hybrid organic-inorganic system according,
to aspect 37 wherein the ions comprise calcium ions,
and wherein the calcium ions comprise Ca’*.

[0252] 40. A hybrid organic-inorganic system according,
to aspect 37, wherein the ions are provided by CaCl,).

[0253] 41. Ahybrid organic-inorganic system according,
to aspect 37, wherein the ions are present in an amount
of at least 0.001% by weight of the substrate.

[0254] 42. Ahybrid organic-inorganic system according
to aspect 41, wherein the ions are present in an amount
of at least 0.005-1.5% by weight of the substrate.

[0255] 43. A hybrid organic-inorganic system according,
to aspect 37, wherein the protein substrate has a thick-
ness of from 0.5 mm-1.5 mm.

[0256] 44. A hybrid organic-inorganic system compris-
ing:

[0257] ordered apatite crystalline structures,

[0258] wherein the ordered apatite crystalline structures
comprise at least one of onion-like, needle-like, flower-
like, and prism-like microstructures; and a protein
substrate capable of growing the ordered apatite crys-
talline structures thereon or therein,

[0259] wherein the protein substrate comprises a poly-
peptide,

[0260] wherein the polypeptide comprises a pentapep-
tide elastin-like-polyptide (ELP) selected from the
group consisting, of
MGSSHHHHHHSSGLVPRGSHMESLLP-[((VPGIG)
,VPGKG(VPGIG),),-DDDEEKFLRRIGRFG-((VP-
GIG)VPGKG(VPGIG),)o13-V,

[0261] wherein the protein substrate comprises an
amount of ions embedded in the protein substrate, and

[0262] wherein the ions embedded in the protein sub-
strate provide nucleation points to allow for selectively
tailoring the ordered apatite crystalline structures.

[0263] 45. A hybrid organic-inorganic system according,
to aspect 44, wherein the ions are selected from a group
consisting of calcium ions, fluoride ions, and zinc oxide
ions.

[0264] 46. A hybrid organic-inorganic system according,
to aspect 44 wherein the ions comprise calcium ions,
and wherein the calcium ions comprise Ca**.

[0265] 47. A hybrid organic-inorganic system according,
to aspect 44, wherein the ions are provided by CaCl,).

[0266] 48. A hybrid organic-inorganic system according,
to aspect 44, wherein the ions are present in an amount
of at least 0.001% by weight of the substrate.

[0267] 49. Ahybrid organic-inorganic system according,
to aspect 48, wherein the ions are present in an amount
of at least 0.005-1.5% by weight of the substrate.

[0268] 50. A hybrid organic-inorganic system according,
to aspect 44, wherein the protein substrate has a thick-
ness of from 0.5 mm-1.5 mm.

EXAMPLES
Membrane Formation:

Example 1

[0269] An ELP and calcium chloride were dissolved in
anhydrous dimethylformamide (DMF) and dimethyl sulfox-
ide (DMSO) in order to form a ELP solution. The ELP was

present in an amount of 5% by weight of the solution and the

calcium chloride was present in an amount of 0.01% by

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13

weight of the solution. The ratio of DMF and DMSO was
9:1. By way of non-limiting example, the ELP may be or
comprise a statherin-ELP. As another example, the ELP may
be or comprise i) a pentapeptide sequence selected from the
group consisting of Gly-X-X-X-X, X-Gly-X-X-X, X-X-
Gly-X-X, X-X-X-Gly-X and X-X-X-X-Gly, (GXXXX,
XGXXX, XXGXX, XXXGX, XXXXG), wherein X is any
amino acid apart from proline, (ii) RGDS-ELP, and/or (iii)
Statherin-ELP. As a further example, the ELP may consist of
or comprise the sequence

MGSSHHHHHHSSGLVPRGSHMESLLP-
[ ((VPGIG) 2VPGKG (VPGIG) 2) 2-

DDDEEKFLRRIGRFG- ( (VPGIG} 2VPGKG (VPGIG} 2} 2]3-v.

[0270] The ELP solution was then mixed with a cross-
linking solution comprising hexamethyl diisocyanate (HDI)
and the solutions were drop casted on a PDMS surface. The
solutions were then left to dry overnight at room temperature
in a low-humidity conditions (less than 20%) inside a
polymer glove box.

Example 2

[0271] An ELP and calcium chloride were dissolved in
DMF and DMSO to form an ELP solution. The ELP was
present in an amount of 5% by weight of the solution and the
calcium chloride was present in an amount of 0.05% by
weight of the solution. The ratio of DMF and DMSO was
9:1.

[0272] The ELP solution was then mixed with a cross-
linker solution comprising HDI and the solutions were drop
casted on a PDMS surface. The solution was then left to dry
overnight at room temperature in a low-humidity conditions
(less than 20%) inside a polymer glove box.

Example 3

[0273] An ELP and calcium chloride was dissolved in
anhydrous DMF and DMSO to form an ELP solution. The
ELP was present in an amount of 5% by weight of the
solution and the calcium chloride was present in an amount
of 0.1% by weight of the solution. The ratio of DMF and
DMSO was 9:1.

[0274] The ELP solution was then mixed with a cross-
linker solution comprising HDI and the solutions were drop
casted on a PDMS surface. The solution was then left to dry
overnight at room temperature in a low-humidity conditions
(less than 20%) inside a polymer glove box.

Example 4

[0275] An ELP and calcium chloride were dissolved in
anhydrous DMF and DMSO to form an ELP solution. The
ELP was present in an amount of 5% by weight of the
solution and the calcium chloride was present in an amount
of 0.5% by weight of the solution. The ratio of DMF and
DMSO was 9:1.

[0276] The ELP solution was then mixed with a cross-
linker solution comprising HDI and the solutions were drop
casted on a PDMS surface. The solution was then left to dry
overnight at room temperature in a low-humidity conditions
(less than 20%) inside a polymer glove box.

Sep. 12, 2024

Example 5

[0277] An ELP and calcium chloride were dissolved in
anhydrous DMF and DMSO to form an ELP solution. The
ELP was present in an amount of 5% by weight of the
solution and the calcium chloride was present in an amount
of 0.5% by weight of the solution. The ratio of DMF and
DMSO was 9:1.

[0278] The ELP solution was then mixed with a cross-
linker solution comprising HDI and the solutions were drop
casted on a PDMS surface. The solution was then left to dry
overnight at room temperature in a low-humidity conditions
(less than 20%) inside a polymer glove box. The resulting
ELP membrane had a thickness of | mm.

Crystal Formation:

Example 6: Onion-Like Shaped Nanocrystals

[0279] The membranes of examples 1-4 were incubated in
a mineralizing solution of 2 mM of hydroxyapatite powder
and 2 mM of sodium fluoride at 37° C. The incubation was
carried out at a pH of 6.0 for a period of 30 days. After 2
days, the pH decreased to around 4 and so the mineralizing
solution was replaced every 2 days in order to restore the pH
to 6.0.

[0280] By replenishing mineralizing solution every 2
days, additional layers of minerals grew on top of the
previous mineralized layer. This grew multiple layers of
crystals on top of each other to create an onion-like struc-
ture. The membranes developed a number of onion-like
shaped nanocrystals in the inside of the membrane as shown
in FIGS. 1A-1B,

[0281] As seen in FIG. 2H, the number of onion-like
nanocrystals decreased as the percentage by weight of
calcium chloride in the membrane increased. For example,
the crystal formed from the membrane described in Example
4 showed the lowest number of onion-like crystals. In
contrast, Example 1 showed the highest number of onion-
like crystals.

[0282] In addition, as shown in FIGS. 3A-3B, the mem-
branes also formed needle shape nanocrystals extending
perpendicularly from the membrane surface. After 30 days
of incubation the needle shaped nanocrystals exhibited a
thickness of around 50 wm. The structures also had improved
mechanical characteristics including stiffness compared to
existing nanocrystals formed from ELP membranes and a
stiffness more similar to natural dental enamel.

Example 7: Flower-Liked Shaped Nanocrystals

[0283] The membranes of examples 1-4 were incubated in
a mineralizing solution of 2 mM of hydroxyapatite powder
and 2 mM of sodium fluoride at 37° C. The incubation was
carried out at a pH of 6.0 for a period of 30 days. The pH
was controlled throughout the incubation period by the
addition of 35 mM Bis-Tri buffer. The mineralizing solution
was replenished after every 6 days.

[0284] The membranes developed a number of flower-
liked shaped nanocrystals in the inside of the membrane as
shown in FIGS. 4A-4F.

[0285] As seen in FIG. 4G, the number of flower-liked
shaped nanocrystals increased, and their size decreased as
the percentage by weight of calcium chloride in the mem-
brane increased. For example, the crystal formed from the
membrane described in Example 4 showed the highest

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number of flower-liked shaped crystal and the smallest
flower-liked shaped nanocrystals. In contrast, Example 1
showed the lowest number of flower-liked shaped crystals
and the largest flower-liked shaped nanocrystals.

[0286] Surprisingly, as shown in FIGS. 4A-4F, the surface
of the membranes did not show any needle shaped nanoc-
rystals on the surface of the membrane as seen in Example

5.

Example 8: Crystal Fusion Inside the Membrane

[0287] The membranes of examples 1-4 were incubated in
a mineralizing solution of 2 mM of hydroxyapatite powder
and 2 mM of sodium fluoride at 37° C. The incubation was
carried out at a pH of 4 for a period of 20 days.

[0288] As shown in FIGS. 5A-5D, a number of crystals
fused inside the membrane.

Example 9: Formation of Crystals Inside Thicker
Membranes

[0289] The membrane of example 5 was incubated in a
mineralizing solution of 0.25 mM of hydroxyapatite powder
and 0.25 mM of sodium fluoride at 37° C. The incubation
was carried out at a pH of 6.0 for a period of 30 days.
[0290] The membrane developed crystal structures inside
the membrane. These crystal structures were observed to
have an increased thickness, as shown in FIGS. 6A-6D.

Example 10: Formation of Crystals Inside Thicker
Membranes

[0291] The membrane of example 5 (comprising 0.5%
CaCl) and 5% ELP having a thickness of 1 mm) was
incubated in a mineralizing solution of 0.5 mM of hydroxy-
apatite powder and 0.5 mM of sodium fluoride at 37° C. The
incubation was carried out at a pH of 6.0 for a period of 30
days.

[0292] The membrane developed crystal structures inside
the membrane. These crystal structures were observed to
have an increased thickness.

[0293] Hydroxyapatite crystals were separately grown by
omitting fluoride ions in the mineralization solution.

Example 11: Coating of 3D Printed Nylon and
Titanium Substrates

[0294] Substrates of titanium and nylon were dipped in a
membrane solution of example 1 and placed on PDMS
surface for drying overnight in a glove box. SEM analysis of
the coated substrates revealed formation of 10 ym thick
coatings formed uniformly over a large surface area, as
shown in FIGS. 9A-9B. The coated substrates were then
placed in a beaker containing mineralizing solution of 2 mM.
hydroxyapatite and 2 mM sodium fluoride 2 mM at pH 6 and
37° C. for 5, 10, and 15 days. The resulting substrates were
analysed for the formation of crystal structures using SEM,
as shown in FIGS. 9A4-9B.

Example 12: Cardiovascular Calcification
Methods and Materials

Elastin Membrane Preparation

[0295] Membranes were fabricated by dissolving com-
mercially available natural elastin (bovine neck ligament,

Sep. 12, 2024

Elastin Products Company—EPC, USA) in 90% anhydrous
dimethylformamide (DMF, Sigma Aldrich, Merck, Ger-
many) and 10% Dimethyl sulfoxide (DMSO, Sigma
Aldrich, Merck, Germany) at room temperature in a low-
humidity conditions (less than 20%) inside a glove box. In
order to crosslink the proteins, hexamethyl diisocyanate
(HDI, Sigma Aldrich, Merck, Germany) was added to pro-
tein solutions for crosslinking at a ratio of 1:3 (lysine to
HDI) and drop-casted on top of Polydimethylsiloxane
(PDMS, Sylgard™ 184 Silicone Elastomer Kit, Dow, USA)
substrate, left to dry overnight. Formed membranes were
washed with deionized water, then they were observed under
polarized light microscope (VHX-S750E, Keyence) with a
cross-polarizer to check the formation of elastin spherulites.

Animal Tissues

[0296] Aorta and mitral valve tissue was harvested from a
bovine heart supplied by a local slaughterhouse. The aorta
samples had a mass of between 45.98-73.42 mg and the
mitral valves a mass of 0.41-9.24 mg. The harvested aorta
and mitral valve samples were stored at -20° C. until use.

Enzymatic Degradation

[0297] Aorta and mitral valve were separated from bovine
heart tissue and were digested by elastase (19.4 U/mg,
Elastin Products Company—EPC, USA) at a concentration
of 1.37 U/ml in 1x phosphate buffered saline (PBS, Sigma
Aldrich, Merck, Germany). Tissues were also digested in
collagenase (125 U/mg, Elastin Products Company—EPC,
USA) at a concentration of 400 U/ml in 1xPBS. The samples
were incubated in enzyme solution for | and 3 hours at 37°
C. Later, they were washed in 1xPBS followed by ultra-pure
water for 20 seconds.

Mineralization,

[0298] The mineralization solution containing hydroxy-
apatite (2 mM) and sodium fluoride (2 mM) were prepared
in deionized water under continuous stirring. Subsequently,
69% (v/v) nitric acid was added dropwise until the powder
was completely dissolved. Later, the pH of the solution was
adjusted to 6.0 by adding 30% (v/v) ammonium hydroxide
(Sigma Aldrich, Merck, Germany) solution. Elastin and
collagen membranes were placed in mineralization solution
(50 ml) and incubated for eight days at 37° C. using a
temperature-controlled incubator (LTE Scientific, Oldham,
UK).

Scanning Electron Microscopy (SEM)

[0299] Samples were mounted on aluminium stubs after
being dried via self-adhesive tape and were coated using an
auto sputter coating machine with a conductive material.
Samples were analyzed using an FEI Inspect F (Hillsboro,
USA). Their surface topography was observed using a
secondary electron detector. A BSE detector was used to
assess the variation in density within each sample. In other
instances, samples were investigated using SEM (Gemini
1525 FEGSEM), operated at 10 kV. The instrument was
equipped with both an inlens detector that recorded second-
ary electrons, and a backscatter electron detector. The DDC-
SEM images were obtained by imaging the same region with
both inlens mode and backscatter mode. Using ImageJ
software, both images were stacked and the inlens image
was assigned to the green channel whereas the backscatter

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image was assigned to the red channel following the tech-
nique reported in Bertazzo et al. 18. Collagen membranes
were mounted on carbon tape and coated with gold layer
using sputter coating (Leica EM ACE600) and were imaged
by JEOL NeoScope JCM 6000Plus (JEOL Ltd., Tokyo,
Japan).

Transmission Electron Microscopy (TEM)

[0300] Aorta tissue was imaged by TEM to analyze its
collagen and elastin content. Tissue sample was embedded
in Araldite resin at room temperature then was cut using a
Ultramicrotome Reichert-Jung E (Leica). After mounting on
a grid, sections were post stained with 2% Uranyl Acetate
and Reynold’s Lead Citrate according to standard method.
Bright-field TEM imaging was performed on a JEM-1230
TEM (JEOL Ltd., Tokyo, Japan) operated at an acceleration
voltage of 80 kV, and the images were recorded by Morada
camera with iTEM software (Olympus-EMSIS).

Histological Analysis

[0301] Digested aorta and mitral valve samples were
embedded in paraffin wax blocks, cut into sections of about
3 um, and stained with Elastin Von Gieson (EVG), Von
Kossa and Masson Trichrome (MT) to visualize under
optical light microscope its elastin content, calcium deposits
and collagen content, respectively.

Results

In-Vitro Models of Elastin

[0302] In order to investigate the capacity of elastin in
directing mineralization, an in-vitro model approach was
used, which has been reported in previous studies to com-
pare the mineralization pattern in elastin. Gourgas, O., et al.,
Biomacromolecules 2019, 20 (7), 2625-2636; Elsharkawy,
S., et al., Nat. Commun. 2018, 9 (1), 2145 Elastin mem-
branes were fabricated HDI crosslinking following our
standard protocol, resulting in transparent membranes (FIG.
19A). As previously observed in ELP membranes32, elastin
membranes also exhibited spherulitic structures throughout
the membrane evidenced by both polarized microscopy
(FIGS. 19A and 19B) and scanning electron microscopy
(SEM) (FIGS. 19D and 198).

[0303] Furthermore, elastin membranes were then
exposed to a mineralization solution for 8 days as previously
described using ELPs. Elsharkawy, S., et al., Nat. Commun.
2018, 9 (1), 2145; Deng, X., et al., Mater. Today Bio 2021,
11, 100119. Interestingly, elastin membranes exhibited a
strong hierarchical mineralization emerging from the bulk of
the membranes that was similar to that previously observed
using ELPs (FIGS. 19D and 19E). In the results, such
spherulitic structures were observed only within and on
elastin membranes, following a similar structure and growth
kinetics as those present in ELP membranes. These results
demonstrate that elastin directs organized mineralization and
acts as a platform for the formation of hierarchical mineral
structures. These data suggest that elastin can be the point of
calcification in soft tissues.

[0304] To test natural elastin mineralization’s role in the
onset of mineralization, investigations were conducted using
bovine aortas and mitral valves. In the anatomy of the aorta,
elastic lamella forms the basic unit of the tissue whereas
collagen fibrils form the interlamellar matrix (FIG. 20).

Sep. 12, 2024

Here, elastic microfibrils are visible as entangled long fila-
ments of about 1 jum diameter (FIGS. 20A and 20B). In the
heart tissue, the organized collagen fibers are aligned par-
allel to the main axis of the smooth muscle cells, which each
fibril formed by uniting each triple helix unit side by side
into bundles (FIGS. 20C and 20D). Dingemans, K. P., et al.,
Anat. Rec. An Off. Publ. Am. Assoc. Anat. 2000, 258 (1),
1-14. Analyzing this further by TEM, it is possible to see that
elastin regions are dense compared to collagen fibers that are
organized in parallel to each other and at multiple orienta-
tions (FIGS. 20E and 20F). On the other hand, heart valves
comprise natural elastin forming a core within elastic fibers
encased by a microfibrillar sheath. Kodigepalli, K. M., et al.,
J. Cardiovasc. Dev. Dis. 2020, 7 (4), 57. Crosslinked elastin
provides astonishing elasticity that endures deformation
under small loads and can shrink back to the initial shape
with minimum energy loss. The outer layer of valves that are
in contact with outflow are formed by densely aligned
collagen fibers that are providing the valves’ strength. The
distribution of both elastin and collagen proteins in heart
tissue and their role in determining the mechanical proper-
ties is exigent. Therefore, elimination of each protein from
the ECM of heart tissue, the changes in mineralization and
mechanical features of the tissue can be studied in relation
to each protein.

[0305] In this study, bovine aorta and mitral valve tissue
samples were used to investigate the effects of both elastin
and collagen in mineralization. To isolate the role of each
protein, the tissues were digested with either elastase to
generate collagen-rich tissues or collagenase to form elastin-
rich tissues. The digestion parameters of concentration,
incubation time, and temperature were adapted from pub-
lished works by Fonck and Greenwald. Fonck, E., et al. Am.
J. Physiol. Heart Circ. Physiol. 2007, 292 (6), H2754-63;
Greenwald, S. E., et al., J. Biomech. Eng. 1997, 119 (4),
438-444, Blastin-stained (Elastin Von Giesen) histological
sections revealed the presence of dark purple elastin fila-
ments in aorta before digestion, which significantly
decreased after digestion with elastase (FIGS. 214-21DD).
FIGS. 21A-21DD shows heart tissues stained for elastin
using Elastin Von Giesen, collagen using Masson’s trichome
and calcium mineral using Von Kossa staining before diges-
tion. Aorta and mitral valves were digested with Elastase and
Collagenase for 1 hour and 3 hours then stained as other
control tissues. In contrast, mitral valves displayed pale
purple staining before digestion due to this tissue’s inher-
ently low content of elastin but is heavy in collagen content
(FIGS. 21A-21DD). In the case of tissues digested with
collagenase, the collagen content (blue/green color by Mas-
son’s Trichrome) decreased in aorta just after 1 hour of
digestion. On the other hand, when the mitral valves were
exposed to collagenase, significant amount of collagen were
degraded. This resulted in drastic decrease in collagen
content, where the mitral valve tissues lost its intactness
(FIGS. 21A-21DD). At this stage of digestion, the elastin
content started to be more visible in darker purple in mitral
valve tissues (FIGS. 21A-21DD). Furthermore, as the mitral
valve tissue is delicate and rich in collagen, after collagenase
digestion, its consistency changed to a gel-like texture.
Although, 3 hours of digestion was not enough to degrade all
collagen and elastin content in both tissues. After the diges-
tion of elastin and collagen contents, each tissue was incu-
bated in mineralization solution for 8 days to further inves-
tigate the calcification ability in soft tissues.

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16

[0306] Both aorta and mitral valve tissues were exposed to
mineralization solution in order to assess their capacity to
mineralize when a specific protein (either collagen or elas-
tin) is isolated in an attempt to better investigate their role in
generating Ca?4deposits (FIGS. 21A-21DD). These depos-
its were more evident in tissues digested by collagenase,
where the elastin content of the ECM remains present
(FIGS. 21A-21DD). Based on observation of Von Kossa
staining of tissues, in both aorta and mitral valve, Ca?*
minerals formed along the elastin fibers (FIGS. 22A-22]
showing higher magnification of tissues). Interestingly, Ca°*
was co-localized with elastin as confirmed by Von Kossa
stain in tissues before and after digestion, specifically the
samples that comprised higher proportions of elastin. (FIGS.
21A-21DD). These results confirm the strong mineralization
potential of elastin and draw attention to its potential in the
early stages of pathological calcification of heart tissues.

[0307] To further investigate the mineralizing role of
elastin, all tissues were then analyzed via SEM observations.
The results confirm the presence of mineral aggregates on
the fibrillar structures of aorta and mitral valve before
enzymatic digestion (FIGS. 23A and 23B). FIGS. 23A-23M.
display SEM images of aorta and mitral valve tissue before
digestion (FIGS. 23A and 23B) showing minerals growing
among the collagen fibers in aorta tissue. Elastin filaments
are more evident in mitral valve tissue. Elastase digestion
after 1 hour (FIGS. 23C and 23D) and 3 hours (FIGS. 23E
and 23F) brings out the collagen fibers. Collagenase diges-
tion after 1 hour (FIGS. 23G and 23H) and 3 hours (FIGS.
231 and 23J) showing heavily mineralized tissues. DDC-

Sep. 12, 2024

[0308] In contrast, tissues that were digested with Elastase
exhibited mineralization alongside the collagen fibrils but at
much lower quantities (FIGS. 23C-F). In collagenase
digested tissues, densely mineralized structures were
observed in both aorta and mitral valves specifically mitral
valves that after just 1 hour of digestion with collagenase
were covered with Ca** minerals (FIG. 23H) and after 3
hours of digestion the mineralization on the tissues was such
that recreated the formations observed on the membrane-like
structures (FIG. 23J) exhibiting spherulitic minerals (FIGS.
23K-23M). Interestingly, these kinds of spherulitic miner-
alized structures resemble those observed in human patho-
logical cardiovascular tissues. Bertazzo, S., et al., Nat.
Mater. 12(6): 576-583 (2013). To further investigate this,
we conducted SEM observations on the mitral valves using,
the backscattered mode, which as expected revealed densely
mineralized regions on the ECM of the tissues after 3-hour
collagenase digestion. (orange area on DDC-SEM micro-
graph, FIG. 23M).

[0309] Table I below provides size measurements of elas-
tin at varied CaCl, concentrations.

TABLE 1

Size measurements analysis of elastin
at different CaCl, concentrations.

Elastin

Mean hydrodynamic

SEM and backscattered images of 3 hours-collagenase radius (nm) Std. dev. Mean PDI
digested mitral valve (FIGS. 23K-23M) highlighting the
Apel 0 mM CaCl, 228.36 124.71 027
dense mineralization, which further analyzed by backscat- 1 mM Cac 1315 Dit 027
tered electron microscopy. However, after digestions, the 10 mM cach, 203.18 14.94 030
mineral growth was again more evident in tissues that were 100 mM CaCl, 3059.42 2206.50 042
digested with collagenase and where elastin fibrils were
more prevalent (FIGS. 23G-23]).
SEQUENCE LISTING
Sequence total quantity: 43
SEQ ID NO: 1 moltype = AA length = 4
FEATURE Location/Qualifiers
REGION 1.4
note = Bioactive epitope
source 1.4
mol_type = protein
organism = synthetic construct
SEQUENCE: 1
RGDS 4
SEQ ID No: 2 moltype = AA length = 15
FEATURE Location/Qualifiers
REGION 1..15
note = statherin-derived peptide
source 1..15
mol_type = protein
organism = synthetic construct
SEQUENCE: 2
DDDEEKFLRR IGRFG 15
SEQ ID NO: 3 moltype = length =
SEQUENCE: 3
000
SEQ ID NO: 4 moltype = length =
SEQUENCE: 4

000

Page 37

US 2024/0301032 Al Sep. 12, 2024

-continued

SEQ ID NO: 5 moltype = length =
SEQUENCE: 5
000
SEQ ID NO: 6 moltype = length =
SEQUENCE: 6
000
SEQ ID No: 7 moltype = length =
SEQUENCE: 7
000
SEQ ID NO: 8 moltype = length =
SEQUENCE: 8
000
SEQ ID NO: 9 moltype = length =
SEQUENCE: 9
000
SEQ ID NO: 10 moltype = length =
SEQUENCE: 10
000
SEQ ID NO: 11 moltype = length =
SEQUENCE: 11
000
SEQ ID NO: 12 moltype = length =
SEQUENCE: 12
000
SEQ ID NO: 13 moltype = length =
SEQUENCE: 13
000
SEQ ID NO: 14 moltype = length =
SEQUENCE: 14
000
SEQ ID NO: 15 moltype = length =
SEQUENCE: 15
000
SEQ ID NO: 16 moltype = length =
SEQUENCE: 16
000
SEQ ID NO: 17 moltype = length =
SEQUENCE: 17
000
SEQ ID No: 18 moltype = AA length = 5
FEATURE Locat ion/Qualifiers
REGION 1.5

note = Tropoelastin recurrent motif
VARIANT 4

note = X is an amino acid selected from the group
consisting of V, P, G, S, F and I
source 1.2.5
mol_type = protein
organism = synthetic construct
SEQUENCE: 18

VPGXG 5
SEQ ID NO: 19 moltype = AA length = 5
FEATURE Locat ion/Qualifiers
REGION 1..5

note = Tropoelastin recurrent motif
VARIANT 4

note = X is any amino acid apart from Proline
source 1.5

mol_type = protein
organism = synthetic construct
SEQUENCE: 19

Page 38

US 2024/0301032 Al Sep. 12, 2024
18

-continued
VPGXG 5
SEQ ID NO: 20 moltype = AA length = 5
FEATURE Location/Qualifiers
REGION 1.5
note = Tropoelastin recurrent motif
REGION 1.5
note = repeat_unit - Motif is to be repeated any number of
times
VARIANT 4
note = X is any amino acid apart from Proline
source 1.5

mol_type = protein
organism = synthetic construct

SEQUENCE: 20
VPGXG 5
SEQ ID NO: 21 moltype = AA length = 5
FEATURE Location/Qualifiers
REGION 1.5
note = Tropoelastin recurrent motif
source 1..5
mol_type = protein
organism = synthetic construct
SEQUENCE: 21
PGIPG 5
SEQ ID NO: 22 moltype = AA length = 5
FEATURE Location/Qualifiers
REGION 1.5
note = Tropoelastin recurrent motif
REGION 1..5
note = repeat_unit - Motif is to be repeated any number of
times
source 1..5

mol_type = protein
organism = synthetic construct
SEQUENCE: 22

PGIPG 5
SEQ ID NO: 23 moltype = AA length = 5
FEATURE Location/Qualifiers
REGION 1.5
note = Tropoelastin recurrent motif
source 1..5

mol_type = protein
organism = synthetic construct
SEQUENCE: 23

PVGSG 5

SEQ ID No: 24 moltype = AA length = 5

FEATURE Location/Qualifiers

REGION 1.5
note = Tropoelastin recurrent motif

REGION 1.5
note = repeat_unit - Motif is to be repeated any number of
times

source 1.5

mol_type = protein
organism = synthetic construct
SEQUENCE: 24

PVGSG 5
SEQ ID NO: 25 moltype = AA length = 5
FEATURE Location/Qualifiers
REGION 1..5
note = Tropoelastin recurrent motif
source 1..5

mol_type = protein
organism = synthetic construct

SEQUENCE: 25

VGEPG 5
SEQ ID NO: 26 moltype = AA length = 5

FEATURE Location/Qualifiers

REGION 1..5

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-continued

note = Tropoelastin recurrent motif

REGION 1..5
note = repeat_unit - Motif is to be repeated any number of
times

source 1..5

mol_type = protein
organism = synthetic construct
SEQUENCE: 26

VGEPG 5
SEQ ID NO: 27 moltype = AA length = 699
FEATURE Location/Qualifiers
REGION 1. .699
note = Peptide sequence
source 1. .699

mol_type = protein
organism = synthetic construct

SEQUENCE: 27

MGSSHHHHHH SSGLVPRGSH MESLLPYPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI 60
GVPGKGYPGI GVPGIGAVTG RGDSPASSVP GIGVPGIGVP GKGVPGIGVP GIGVPGIGVP 120
GIGVPGKGVP GIGVPGIGVP GIGVPGIGVP GKGVPGIGVP GIGVPGIGVP GIGVPGKGVP 180
GIGVPGIGAV TGRGDSPASS VPGIGVPGIG VPGKGYPGIG VPGIGVPGIG VPGIGVPGKG 240
VPGIGVPGIG VPGIGVPGIG VPGKGVPGIG VPGIGYPGIG VPGIGVPGKG VPGIGVPGIG 300
AVIGRGDSPA SSVPGIGVPG IGVPGKGVPG IGVPGIGVPG IGVPGIGVPG KGVPGIGVPG 360
IGVPGIGVPG IGVPGKGVPG IGVPGIGVPG IGVPGIGVPG KGVPGIGVPG IGAVTGRGDS 420
PASSVPGIGV PGIGVPGKGV PGIGVPGIGV PGIGVPGIGV PGKGVPGIGV PGIGVPGIGV 480
PGIGVPGKGV PGIGVPGIGV PGIGVPGIGV PGKGVPGIGV PGIGAVTGRG DSPASSVPGI 540
GVPGIGYPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK 600
GVPGIGYPGI GVPGIGVPGI GVPGKGVPGI GVPGIGAVTG RGDSPASSVP GIGVPGIGVP 660

GKGVPGIGVP GIGVPGIGVP GIGVPGKGVP GIGVPGIGV 699
SEQ ID NO: 28 moltype = AA length = 877
FEATURE Locat ion/Qualifiers
REGION 1..877
note = Peptide sequence
source 1..877

mol_type = protein

organism = synthetic construct
SEQUENCE: 28
MESLLPYPGI GVPGIGVPGK GVPGIGVPGI GEEIQIGHIP REDVDYHLYP VPGIGVPGIG 60
VPGKGVPGIG VPGIGVGVAP GVGVAPGVGV APGVPGIGVP GIGVPGKGVP GIGVPGIGEE 120
IQIGHIPRED VDYHLYPVPG IGVPGIGVPG KGVPGIGVPG IGVGVAPGVG VAPGVGVAPG 180
VPGIGVPGIG VPGKGVPGIG VPGIGEEIQI GHIPREDVDY HLYPVPGIGV PGIGVPGKGV 240
PGIGVPGIGV GVAPGVGVAP GVGVAPGVPG IGVPGIGVPG KGVPGIGVPG IGEEIQIGHI 300
PREDVDYHLY PVPGIGVPGI GVPGKGVPGI GVPGIGVGVA PGVGVAPGVG VAPGVPGIGV 360
PGIGVPGKGV PGIGVPGIGE EIQIGHIPRE DVDYHLYPVP GIGVPGIGVP GKGVPGIGVP 420
GIGVGVAPGV GVAPGVGVAP GVPGIGVPGI GVPGKGVPGI GVPGIGEEIQ IGHIPREDVD 480
YHLYPVPGIG VPGIGVPGKG VPGIGVPGIG VGVAPGVGVA PGVGVAPGVP GIGVPGIGVP 540
GKGVPGIGVP GIGEEIQIGH IPREDVDYHL YPVPGIGVPG IGVPGKGVPG IGVPGIGVGY 600
APGVGVAPGV GVAPGVPGIG VPGIGVPGKG VPGIGVPGIG EEIQIGHIPR EDVDYHLYPV 660
PGIGVPGIGV PGKGVPGIGV PGIGVGVAPG VGVAPGVGVA PGVPGIGVPG IGVPGKGVPG 720
IGVPGIGEEI QIGHIPREDV DYHLYPVPGI GVPGIGVPGK GVPGIGVPGI GVGVAPGVGV 780
APGVGVAPGV PGIGVPGIGV PGKGVPGIGV PGIGEEIQIG HIPREDVDYH LYPVPGIGVP 840

GIGVPGKGVP GIGVPGIGVG VAPGVGVAPG VGVAPGV 877
SEQ ID NO: 29 moltype = AA length = 1107
FEATURE Locat ion/Qualifiers
REGION 1..1107
note = Peptide sequence
source 1..1107

mol_type = protein

organism = synthetic construct
SEQUENCE: 29
MESLLPVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV 60
GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGY GVPGVGVPGE 120
GVPGVGVPGV GVPGVGVPGY GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV 180
GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGY GvPGvGvPGV 240
GVPGEGVPGV GVPGVGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP 300
GVGIPGYGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP 360
GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP 420
GVGIPGYGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP 480
GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP GVGIPGVGIP 540
GVGIPGVYGIP GVGIPGVPGVY GVPGVGVPGE GVPGYGVPGV GVPGVGVPGV GVPGEGVPGV 600
GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV 660
GVPGVGVPGE GVPGVGVPGVY GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE 720
GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV 780

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GVPGVGVPGV
GVGIPGVGIP
GVGIPGVGIP
GVGIPGVGIP
GVGIPGYGIP
GVGIPGYGIP

GVPGEGVPGV
GVGIPGVGIP
GVGIPGVGIP
GVGIPGVGIP
GVGIPGVGIP
GVGIPGVGIP

SEQ ID NO: 30
FEATURE
REGION

source

SEQUENCE: 30
MESLLPVPGI GVPGIGVPGK
GVPGIGYPGK GVPGIGVPGI
GVPGIGYPGI GVPGIGVPGI
GVPGIGYPGI GVPGKGVPGI
GVPGKGYPGI GVPGIGVPGI
GVPGIGVPGI GVPGIGVPGK
GVPGIGVYPGK GVPGIGVPGI
GVPGIGVYPGI GVPGIGVPGI
GVPGIGVPGI GVPGKGVPGI
GVPGKGVPGI GVPGIGVPGI
GVPGIGV

SEQ ID No:
FEATURE
REGION

31

source

SEQUENCE: 31
VPGVGVPGVG VPGEGVPGVG
VPGEGVPGVG VPGVGVPGVG
VPGVGVPGVG VPGVGVPGEG
VPGVGVPGEG VPGVGVPGVG
VPGVGVPGVG
VPEGEGVPGVG
VPGEGVPGVG VPGVGV
SEQ ID NO
FEATURE
REGION

32

source

SEQUENCE: 32

MESLLPVPGI GVPGIGVPGK
EKFLRRIGRF GVPGIGVPGI
GVPGIGVPGI GVPGKGVPGI
RIGRFGVPGI GVPGIGVPGK
GVPGIGVPGK GVPGIGVPGI
GVPGIGVPGI GVPGKGVPGI

SEQ ID NO:
FEATURE
REGION

33

source

SEQUENCE
MESLLPVPGI
EKFLRRIGRF
GVPGIGVPGI
RIGRFGVPGL
GVPGIGYPGK
GVPGIGVPGI
GVPAVGYPAV
GVPAVGVPAV

33
GVPGIGVPGK
GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGK.
GVPGIGVPGI
GVPGKGVPGI
GVPAVGVPAV
GVPAVGVPAV

SEQ ID NO: 34

GVPGVGVGIP
GVGIPGVGIP
GVGIPGVGIP
GVGIPGVGIP
GVGIPGYGIP
GVGIPGY

GVGIPGVGIP GVGIPGVGIP
GVGIPGVGIP GVGIPGVGIP
GVGIPGVGIP GVGIPGVGIP
GVGIPGVGIP GVGIPGVGIP
GVGIPGVGIP GVGIPGVGIP

moltype = AA length = 607
Locat ion/Qualifiers

1..607

note = Peptide sequence
1..607
mol_type =
organism =

protein
synthetic construct
GVPGIGVPGI
GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGIGYPGI
GVPGKGVPGI
GVPGIGVPGI
GVPGIGVPGK

GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI

GVPGKGVPGI
GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGIGVPGI

moltype = AA length = 376
Location/Qualifiers

1.376
note =
1. .376
mol_type =
organism =

Protein sequence

protein
synthetic construct

VPGVGVPGVG
VPGVGVPGEG
VPGVGVPGVG
VPGVGVPGVG
VPGEGVPGVG
VPGVGVPGVG

VPGVGVPGEG VPGVGVPGVG
VPGVGVPGVG VPGVGVPGVG
VPGVGVPGVG VPGEGVPGVG
VPGEGVPGVG VPGVGVPGVG
VPGVGVPGVG VPGVGVPGEG
VPEGVGVPGEG VPGVGVPGVG

moltype = AA length = 352
Location/Qualifiers

1. .352
note =
1. .352
mol_type =
organism =

Peptide sequence

protein

synthetic construct
GVPGIGYPGI
GVPGKGYPGI
GVPGIGYPGI
GVPGIGVPGI
GVPGIGVPGI
GVPGIGVPGI

GVPGIGVPGI
GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGK

GVPGKGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGKGVPGI
GVPGIGDDDE
GVPGIGVPGI
moltype = AA length = 452
Location/Qualifiers

1. .452
note =
1.452
mol_type = protein
organism = synthetic

Peptide sequence

construct

GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGI
GVPGIGVPGL
GVPGIGVPGI
GVPGIGVPGI
GVPAVGYPAV
GVPAVGVPAV

GVPGIGVPGI
GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGK
GVPAVGVPAV
og

GVPGKGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGKGVPGI
GVPGIGDDDE
GVPGIGVPGI
GVPAVGVPAV

moltype = AA length = 797

GVGIPGVGIP
GVGIPGVGIP
GVGIPGVGIP
GVGIPGVGIP
GYGIPGVGIP

GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGIGVPGI
GVPGKGVPGI
GVPGIGVPGI
GVPGIGVPGK
GVPGIGVPGI
GVPGIGVPGI
GVPGKGVPGI

VPGVGVPGVG
VPGEGVPGVG
VPGVGVPGVG
VPGVGVPGEG
VPEGVGYPGVG
VPEGVGYPGVG

GVPGIGDDDE
GVPGIGVEGI
GDDDEEKFLR
GVPGIGVPGI
EKFLRRIGREF
ow

GVPGIGDDDE
GVPGIGVPGI
GDDDEEKFLR
GVPGIGVPGI
EKFLRRIGRE
GVPAVGVPAV
GVPAVGVPAV

60

120
180
240
300
360
420
480
540

607

60
120
180
240
300

376

60

120
180
240
300
352

60

120
180
240
300
360
420
452

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FEATURE Locat ion/Qualifiers
REGION 1..797
note = Peptide sequence
source 1..797

mol_type = protein

organism = synthetic construct
SEQUENCE: 34
MESLLPYPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGDDDE
EKPLRRIGRF GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI
GVPGIGYPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI GDDDEEKFLR
RIGRFGYPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI
GVPGIGYPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGDDDE EKFLRRIGRF
GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI
GVPGIGVPGK GVPGIGVPGI GDDDEEKFLR RIGRFGVPGI GVPGIGVPGK GVPGIGVPGI
GVPGIGYPGI GVPGKGVPGI GVPGIGYPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI
GVPGKGYPGI GVPGIGDDDE EKFLRRIGRF GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI
GVPGIGYPGK GVPGIGVPGI GVPGIGYPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK
GVPGIGYPGI GDDDEEKFLR RIGRFGVPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI
GVPGKGVPGI GVPGIGV

SEQ ID NO: 35 moltype = AA length = 457
FEATURE Location/Qualifiers
REGION 1. .457

note = Peptide sequence
source 1. .457

mol_type = protein

organism = synthetic construct
SEQUENCE: 35
MESLLPYPGV GVPGVGVPGE GVPGVGVPGV GVPGYGVPGV GVPGEGVPGY GVPGVGVPGY
GVPGVGYPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE
GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV
GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV
GVPGEGVPGV GVPGVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGV

SEQ ID NO: 36 moltype = AA length = 557
FEATURE Location/Qualifiers
REGION 1.557

note = Peptide sequence
source 1..557

mol_type = protein

organism = synthetic construct
SEQUENCE: 36
MESLLPVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV
GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGY GVPGVGVPGV GVPGVGVPGE
GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV
GVPGVGYPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV
GVPGEGYPGV GVPGVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGYPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGYPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGV

SEQ ID NO: 37 moltype = AA length = 707
FEATURE Location/Qualifiers
REGION 1..707

note = Peptide sequence
source 1..707

mol_type = protein

organism = synthetic construct
SEQUENCE: 37
MESLLPVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPCV
GVPGVGYPGE GVPGVGYPGV GVPGVGVPGY GVPGEGVPGV GVPGVGVPGV GVPGYGVPGE
GVPGVGYPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPCV
GVPGVGYPGV GVPGEGVPGV GVPGVGVPGY GVPGVGVPGE GVPGVGVPGV GvPGYGVPC
GVPGEGYPGY GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGY
GVPGVGYPGY GVPGVGVPGE GVPCVGVPCY GVPGVCVPGV GVPGECVPGY GVPGYGVPCY
GVPGVGVYPGE GVPGVGVPGVY GVPGVGVPGV GVPGEGVPGVY GVPGVGVPGV GVPGYGVPGE
GVPGVGVPGV GVPGVGVPGY GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV
GVPGVGVPGV GVPGEGVPGY GVPGVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV

60

120
180
240
300
360
420
487

60

120
180
240
300
360
420
480
540
600

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Sep. 12, 2024

GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV GVPAVGVPAV

SEQ ID NO: 38 moltype = AA length
FEATURE Location/Qualifiers
REGION 1..707

GVPAVGVPAV GVPAVGVPAV
GvPAVGV

= 707

note = Peptide sequence

source 1..707
mol_type = protein
organism = synthetic

SEQUENCE: 38

MESLLPVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV

GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV

GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV

GVPGVGVPGV GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE

GVPGEGVPGV GVPGVGVPAV GVPAVGVPAV GVPAVGVPAV

GVPAVGYPAV GVPAVGVPAV GVPAVGYPAV GVPAVGVPAV

GVPAVGYPAV GVPAVGVPAV GVPAVGYPAV GVPAVGVPAV

GVPAVGYPAV GVPAVGVPAV GVPAVGYPAV GVPAVGVPGV

GVPGVGYPGV GVPGEGVPGV GVPGVGYPGV GVPGYGVPGE

GVPGEGVPGV GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV

GVPGVGVPGV GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV

GVPGVGVPGE GVPGVGVPGV GVPGVGVPGV GVPGEGVPGV

SEQ ID NO: 39 moltype = AA length
FEATURE Location/Qualifiers
REGION 1.698

construct

GVPGEGVPGV GVPGVGVPGV
GVPGVGVPGV GVPGYGVPGE
GVPGVGVPGE GVPGYGVPGV
GVPGVGVPGV GVPGVGVPGV
GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV
GVPAVGVPAV GVPAVGVPAV
GVPGVGVPGE GVPGYGVPGV
GVPGVGVPGV GVPGYGVPGV
GVPGVGVPGV GVPGEGVPGV
GVPGEGVPGV GVPGVGVPGV
evpcvey

= 698

note = Bioactive sequence

source 1. .698
mol_type = protein
organism = synthetic

SEQUENCE: 39

MGSSHHHHHH SSGLVPRGSH MESLLPVPGI GVPGIGVPGK

GVPGKGYPGI GVPGIGAVTG RGDSPASSVP GIGVPGIGVP

GIGVPGKGVP GIGVPGIGVP GIGVPGIGVP GKGVPGIGVP

GIGVPGIGAV TGRGDSPASS VPGIGVPGIG VPGKGVPGIG

VPGIGVPGIG VPGIGVPGIG VPGKGVPGIG VPGIGVPGIG

AVTGRGDSPA SSVPGIGVPG IGVPGKGVPG IGVPGIGVPG

IGVPGIGVPG IGVPGKGVPG IGVPGIGVPG IGVPGIGVPG

PASSVPGIGV PGIGVPGKGV PGIGVPGIGY PGIGVPGIGY

PGIGVPGKGY PGIGVPGIGV PGIGVPGIGY PGKGVPGIGY

GVPGIGYPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI

GVPGIGYPGI GVPGIGVPGI GVPGKGVPGI GVPGIGAVTG

GKGVPGIGVP GIGVPGIGVP GIGVPGKGVP GIGVPGIG

SEQ ID NO: 40 moltype = AA length
FEATURE Locat ion/Qualifiers
REGION 1. .606

construct

GVPGIGVPGI GVPGIGVPGI
GKGVPGIGVP GIGVPGIGVP
GIGVPGIGVP GIGVPGKGVP
VPGIGVPGIG VPGIGVPGKG
VPGIGVPGKG VPGIGVPGIG
IGVPGIGVPG KGVPGIGVPG
KGVPGIGVPG IGAVTGRGDS
PGKGVPGIGV PGIGVPGIGV
PGIGAVTGRG DSPASSVPGI
GVPGIGVPGI GVPGIGVPGK
RGDSPASSVP GIGVPGIGVP

= 606

note = ELP membrane sequence

source 1. .606

mol_type = protein

organism = synthetic
SEQUENCE: 40
MESLLPYPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI
GVPGIGYPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI
GVPGIGYPGI GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI
GVPGIGYPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK
GVPGKGYPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI
GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI
GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI
GVPGIGVYPGI GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI
GVPGIGVYPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK
GVPGKGYPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI
GVPGIG

SEQ ID NO: 41 moltype = AA length
FEATURE Locat ion/Qualifiers
REGION 1. .351

construct

GVPGKGVPGI GVPGIGVPGI
GVPGIGVPGI GVPGIGVPGK
GVPGIGVPGK GVPGIGVPGI
GVPGIGVPGI GVPGIGVPGI
GVPGIGVPGI GVPGKGVPGI
GVPGKGVPGI GVPGIGVPGI
GVPGIGVPGI GVPGIGVPGK
GVPGIGVPGK GVPGIGVPGI
GVPGIGVPGI GVPGIGVPGI
GVPGIGVPGI GVPGKGVPGI

= 351

note = ELP membrane sequence

source 1..351
mol_type = protein
organism = synthetic
SEQUENCE: 41
MESLLPVPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI
EKELRRIGRF GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI
GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK

construct

GVPGKGVPGI GVPGIGDDDE
GVPGIGVPGK GVPGIGVPGI
GVPGIGVPGI GDDDEEKFLR

660
707

707

60

120
180
240
300
360
420
480
540
600
606

60
120
180

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RIGRFGVPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI
GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGDDDE EKFLRRIGRF
GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI G

240
351

SEQ ID NO: 42 moltype = AA length = 914
FEATURE Location/Qualifiers
REGION 1..914

note = ELP membrane sequence
source 1..914

mol_type = protein

organism = synthetic construct
SEQUENCE: 42
MESLLPVPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGDDDE 60
EKFLRRIGRF GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI
GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI GDDDEEKFLR
RIGRFGVPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI
GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGDDDE EKFLRRIGRF
GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI
GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK GVPGIGVPGI GDDDEEKFLR RIGRFGVPGI
GVPGIGVPGK GVPGIGVPGI GVPGIGVPGI GVPGKGVPGI GVPGIGVPGI GVPGIGVPGK
GVPGIGYPGI GVPGIGVPGI GVPGKGVPGI GVPGIGAVTG RGDSPASSVP GIGVPGIGVP
GKGVPGIGVP GIGVPGIGVP GIGVPGKGVP GIGVPGIGVP GIGVPGIGVP GKGVPGIGVP
GIGVPGIGVP GIGVPGKGVP GIGVPGIGAV TGRGDSPASS VPGIGVPGIG VPGKGVPGIG
VPGIGYPGIG VPGIGVPGKG VPGIGVPGIG VPGIGVPGIG VPGKGVPGIG VPGIGVPGIG
VPGIGVPGKG VPGIGVPGIG AVTGRGDSPA SSVPGIGYPG IGVPGKGVPG IGVPGIGVPG
IGVPGIGVPG KGVPGIGVPG IGVPGIGVPG IGVPGKGVPG IGVPGIGVPG IGVPGIGVPG
KGVPGIGVPG IGAVTGRGDS PASSVPGIGV PGIGVPGKGV PGIGVPGIGV PGIGVPGIGV
PGKGVPGIGY PGIG 914

360

"
a

SEQ ID NO: 43 moltype = AA length
FEATURE Location/Qualifiers
REGION 1..5

note = Tropoelastin recurrent motif
source 1..5

mol_type = protein

organism = synthetic construct
SEQUENCE: 43
VPGIG 5

1. A polypeptide substrate comprising calcium ions,
wherein the calcium ions are embedded within the polypep-
tide substrate.

2. A substrate according to claim 1 wherein the calcium
ions are Ca?*.

3. A substrate according to claim 1, wherein the calcium
ions are provided by CaCl.

4. A substrate according to claim 1, wherein the calcium
ions are present in an amount of at least 0.001% by weight
of the substrate.

5. A substrate according to claim 4, wherein the calcium
ions are present in an amount of at least 0.005-1.5% by
weight of the substrate.

6. A substrate according to claim 1, wherein the polypep-
tide is a pentapeptide Elastin-like-polyptide selected from
the group consisting of Gly-X-X-X-X, X-Gly-X-X-X, X-X-
Gly-X-X, X-X-X-Gly-X and X-X-X-X-Gly, (GXXXX,
XGXXX, XXGXX, XXXGX, XXXXG), wherein X is any
amino acid apart from proline.

7. A substrate according to claim 1, wherein the polypep-
tide is

MGSSHHHHHHSSGLVPRGSHMESLLP-
[ ((VPGIG) 2VPGKG (VPGIG) 2) 2-

DDDEEKFLRRIGRFG- ( (VPGIG} 2VPGKG (VPGIG} 2} 2]3-v.

8. A substrate according to claim 1, wherein the polypep-
tide substrate has a thickness of from 0.5 mm-1.5 mm.

9. A process for forming an elastin-like polypeptide
membrane according to claim 1, the process comprising the
steps of:

a) dissolving elastin-like polypeptides with a source of

calcium ions and a solvent to form an ELP solution; and

b) applying the solution onto a surface to form a mem-

brane.

10. A process according to claim 9, wherein the ELP is
present in an amount of from 1-20% by weight of the
solution.

11. A process according to claim 9, wherein the source of
calcium ions may be present in an amount of 0.005-1.5% by
volume of the solution.

12. A process according to claim 9, wherein the step a)
further comprises the step of mixing the ELP solution with
a cross-linker.

13. A process according to claim 12, wherein the cross-
linker is hexamethyl diisocyanate.

14. A crystal formed from and at least partly embedded in
a substrate according to claim 1.

15. A crystal according to claim 14, wherein the crystal is
located at least partly inside the bulk of the polypeptide
substrate.

16. A crystal according to claim 14, wherein the crystal is
located partly inside the bulk of the polypeptide substrate
and partly on the surface of the polypeptide substrate.

Page 44

US 2024/0301032 Al Sep. 12, 2024
24

17. A crystal according to claim 14, wherein the crystal
has a hierarchical structure.

18. A crystal according to claim 14, wherein the crystal
comprises nanocrystals.

19. A crystal according to claim 18, wherein the nanoc-
rystals are arranged in concentric layers.

20. A crystal according to claim 18, wherein the nanoc-
rystals have a needle shape.

21. A crystal according to claim 20, wherein the needle
shaped nanocrystals are located on the polypeptide substrate
surface and orientated perpendicular to the polypeptide
substrate surface

22. A crystal according to claim 18, wherein the nanoc-
rystals have a flower-liked shaped.

23. A crystal according to claim 18, wherein the nanoc-
rystals within the substrate are fused.

24. A process for producing a crystal according to claim
14 comprising the steps of contacting a polypeptide sub-
strate with a mineralizing solution.

eR eRe
Source notes & attribution
  1. https://rexresearch.com/ChenHasanToothRegeneration/US2024301032A1.pdf

Dossier visual record.

All 1 figures

Source illustrations for Rebuilding enamel. Captions identify the document and evidence type.

Keep following.

Thematic connections, not evidence of a shared mechanism